Efficacy and safety of vamorolone in Duchenne muscular dystrophy: An 18-month interim analysis of a non-randomized open-label extension study

• Edward C. Smith,

  Roles Investigation, Writing – review & editing

  Affiliation Duke University, Durham, North Carolina, United States of America

  http://orcid.org/0000-0003-0073-9377

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• Laurie S. Conklin,

  Roles Data curation, Formal analysis, Writing – original draft, Writing – review & editing

  Affiliations ReveraGen Biopharma, Rockville, Maryland, United States of America, Children’s National Hospital, Washington, District of Columbia, United States of America

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• Eric P. Hoffman,

  Roles Conceptualization, Formal analysis, Funding acquisition, Methodology, Writing – original draft, Writing – review & editing

  Affiliations ReveraGen Biopharma, Rockville, Maryland, United States of America, Binghamton University–SUNY, Binghamton, New York, United States of America

  http://orcid.org/0000-0001-6470-5139

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• Paula R. Clemens,

  Roles Conceptualization, Data curation, Project administration, Writing – original draft, Writing – review & editing

  Affiliation University of Pittsburgh and Department of Veterans Affairs Medical Center, Pittsburgh, Pennsylvania, United States of America

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• Jean K. Mah,

  Roles Investigation, Project administration, Writing – review & editing

  Affiliation Alberta Children’s Hospital, Calgary, Alberta, Canada

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• Richard S. Finkel,

  Roles Investigation, Project administration, Writing – review & editing

  Affiliation Nemours Children’s Hospital, Orlando, Florida, United States of America

  http://orcid.org/0000-0002-9351-7054

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• Michela Guglieri,

  Roles Investigation, Project administration, Writing – review & editing

  Affiliation John Walton Muscular Dystrophy Research Centre, Newcastle University, Newcastle upon Tyne Hospitals NHS Foundation Trust, Newcastle upon Tyne, United Kingdom

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• Mar Tulinius,

  Roles Investigation, Project administration, Writing – original draft, Writing – review & editing

  Affiliation Queen Silvia Children’s Hospital, Gothenburg, Sweden

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• Yoram Nevo,

  Roles Investigation, Project administration, Writing – review & editing

  Affiliation Schneider Children’s Medical Center, Tel Aviv University, Petah Tikvah, Israel

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• Monique M. Ryan,

  Roles Investigation, Project administration, Writing – review & editing

  Affiliation Royal Children’s Hospital and Murdoch Children’s Research Institute, Melbourne, Victoria, Australia

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• Richard Webster,

  Roles Investigation, Project administration, Writing – review & editing

  Affiliation The Children’s Hospital at Westmead, Sydney, New South Wales, Australia

  http://orcid.org/0000-0002-8198-2207

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• Diana Castro,

  Roles Investigation, Project administration, Writing – review & editing

  Affiliation University of Texas Southwestern Medical Center, Dallas, Texas, United States of America

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• Nancy L. Kuntz,

  Roles Investigation, Project administration, Writing – review & editing

  Affiliation Ann & Robert H. Lurie Children’s Hospital of Chicago, Chicago, Illinois, United States of America

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• Laurie Kerchner,

  Roles Project administration, Supervision, Writing – review & editing

  Affiliation TRiNDS, Pittsburgh, Pennsylvania, United States of America

  http://orcid.org/0000-0003-0690-5786

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• Lauren P. Morgenroth,

  Roles Data curation, Project administration, Writing – review & editing

  Affiliation TRiNDS, Pittsburgh, Pennsylvania, United States of America

  ⨯
• Adrienne Arrieta,

  Roles Data curation, Project administration, Writing – review & editing

  Affiliation TRiNDS, Pittsburgh, Pennsylvania, United States of America

  http://orcid.org/0000-0002-2583-8585

  ⨯
• Maya Shimony,

  Roles Data curation, Project administration, Writing – review & editing

  Affiliation TRiNDS, Pittsburgh, Pennsylvania, United States of America

  ⨯
• Mark Jaros,

  Roles Formal analysis, Validation, Writing – review & editing

  Affiliation Summit Analytical, Denver, Colorado, United States of America

  ⨯
• Phil Shale,

  Roles Data curation, Formal analysis, Writing – review & editing

  Affiliation Summit Analytical, Denver, Colorado, United States of America

  http://orcid.org/0000-0001-6910-1174

  ⨯
• Heather Gordish-Dressman,

  Roles Conceptualization, Data curation, Formal analysis, Project administration, Supervision, Writing – original draft, Writing – review & editing

  Affiliation Children’s National Hospital, Washington, District of Columbia, United States of America

  http://orcid.org/0000-0002-2330-5427

  ⨯
• Laura Hagerty,

  Roles Data curation, Formal analysis, Writing – review & editing

  Affiliation ReveraGen Biopharma, Rockville, Maryland, United States of America

  http://orcid.org/0000-0001-6341-0697

  ⨯
• Utkarsh J. Dang,

  Roles Data curation, Formal analysis, Writing – review & editing

  Affiliation Binghamton University–SUNY, Binghamton, New York, United States of America

  http://orcid.org/0000-0003-4120-2015

  ⨯
• Jesse M. Damsker,

  Roles Data curation, Formal analysis, Supervision, Writing – review & editing

  Affiliation ReveraGen Biopharma, Rockville, Maryland, United States of America

  ⨯
• Benjamin D. Schwartz,

  Roles Conceptualization, Formal analysis, Methodology, Project administration, Supervision, Writing – review & editing

  Affiliation Camden Group, St. Louis, Missouri, United States of America

  http://orcid.org/0000-0003-1163-9478

  ⨯
• Laurel J. Mengle-Gaw,

  Roles Conceptualization, Formal analysis, Project administration, Supervision, Writing – review & editing

  Affiliation Camden Group, St. Louis, Missouri, United States of America

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• Craig M. McDonald ,

  Roles Investigation, Writing – review & editing

  * E-mail: cmmcdonald@ucdavis.edu

  Affiliation University of California, Davis, Davis, California, United States of America

  http://orcid.org/0000-0002-8779-3220

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• the CINRG VBP15 and DNHS Investigators
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