Download Citation
Article Source:
Efficacy and safety of vamorolone in Duchenne muscular dystrophy: An 18-month interim analysis of a non-randomized open-label extension study
Smith EC,
Conklin LS,
Hoffman EP,
Clemens PR,
Mah JK,
et al.
(2020)
Efficacy and safety of vamorolone in Duchenne muscular dystrophy: An 18-month interim analysis of a non-randomized open-label extension study.
PLOS Medicine 17(9): e1003222.
https://doi.org/10.1371/journal.pmed.1003222