Characterization of hydroxypropyl-beta-cyclodextrins used in the treatment of Niemann-Pick Disease type C1

Open Access

Peer-reviewed

Research Article

Alfred L. Yergey ,

* E-mail: alyergey@gmail.com

Affiliation Eunice Kennedy Shriver National Institute of Child Health and Human Development, National Institutes of Health, Bethesda, MD, United States of America

http://orcid.org/0000-0002-1233-6981

⨯
Paul S. Blank,

Affiliation Eunice Kennedy Shriver National Institute of Child Health and Human Development, National Institutes of Health, Bethesda, MD, United States of America
⨯
Stephanie M. Cologna,

Affiliation Department of Chemistry, University of Illinois at Chicago, Chicago, IL, United States of America
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Peter S. Backlund,

Affiliation Eunice Kennedy Shriver National Institute of Child Health and Human Development, National Institutes of Health, Bethesda, MD, United States of America
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Forbes D. Porter,

Affiliation Eunice Kennedy Shriver National Institute of Child Health and Human Development, National Institutes of Health, Bethesda, MD, United States of America
⨯
Allan J. Darling

Affiliation Vtesse, Inc., Gaithersburg, MD, United States of America
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