Duchenne muscular dystrophy

A shape-based functional index for objective assessment of pediatric motor function

Shashwat Kumar, Arafat Rahman, [ ... ], Laura E. Barnes

Predicting trajectories of the north star ambulatory assessment total score in Duchenne muscular dystrophy

Francesco Muntoni, James Signorovitch, [ ... ], Craig McDonald

The prospective acceptability of preventative IV bisphosphonate therapy prior to fracture: Perspectives of young people with Duchenne muscular dystrophy, parents and health professionals

Danielle C. Mountain, Nicola Crabtree, [ ... ], Lucy Bray

Longitudinal trajectories of muscle impairments in growing boys with Duchenne muscular dystrophy

Ines Vandekerckhove, Marleen Van den Hauwe, [ ... ], Kaat Desloovere

Identification of suitable qPCR reference genes for the normalization of gene expression in the BL10-mdx and D2-mdx mouse models of Duchenne muscular dystrophy

Kayleigh Putker, Anne-Fleur Schneider, [ ... ], Maaike van Putten

Respiratory pathology in the mdx/utrn ^-/- mouse: A murine model for Duchenne Muscular Dystrophy (DMD)

Marán Y. Hernández Rodríguez, Debolina D. Biswas, [ ... ], Mai K. ElMallah

Navigating adulthood: Exploring the transition needs of adolescents and young adults affected by Duchenne or Becker muscular dystrophy

Sharon Barak, Shirley Ackerman Laufer, [ ... ], Tali Kaplan

Height development and multiple bone health indicators in children aged 2–12 years with Duchenne muscular dystrophy (DMD)

Bingying Wang, Linyuhan Zhou, [ ... ], Xiaomei Sun

Determination of qPCR reference genes suitable for normalizing gene expression in a novel model of Duchenne muscular dystrophy, the D2-mdx mouse

Brigida Boccanegra, Roberta Lenti, [ ... ], Annamaria De Luca

Characterization of patients with Duchenne muscular dystrophy across previously developed health states

Francesco Muntoni, Nathalie Goemans, [ ... ], the PRO-DMD-01 study, the Imaging DMD study, iMDEX, the collaborative Trajectory Analysis Project (cTAP)

Distribution of MRI-derived T2 values as a biomarker for in vivo rapid screening of phenotype severity in mdx mice

Emily A. Waters, Chad R. Haney, [ ... ], Alexis R. Demonbreun

Meaningful changes in motor function in Duchenne muscular dystrophy (DMD): A multi-center study

Francesco Muntoni, James Signorovitch, [ ... ], cTAP

Functional trajectories before and after loss of ambulation in Duchenne muscular dystrophy and implications for clinical trials

Craig M. McDonald, James Signorovitch, [ ... ], Investigators from the PRO-DMD-01 Study, Collaborative Trajectory Analysis Project (cTAP)

Duchenne muscular dystrophy

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