About the Authors

Stefania Zampieri

Affiliation Regional Coordinator Center for Rare Diseases, University Hospital Santa Maria della Misericordia, Udine, Italy

Silvia Cattarossi

Affiliation Regional Coordinator Center for Rare Diseases, University Hospital Santa Maria della Misericordia, Udine, Italy

Ana Maria Oller Ramirez

Affiliation Centro de Estudio de las Metabolopatias Congénitas, CEMECO, University of Córdoba, Córdoba, Argentine

Camillo Rosano

Affiliation Patologia Molecolare Integrata – A.O.U. IRCSS San Martino – IST, Istituto Nazionale per la Ricerca sul Cancro, Genova, Italy

Charles Marques Lourenco

Affiliation Medical Genetics Service, Clinics Hospital of Ribeirao Preto, University of Sao Paulo, Sao Paulo, Brazil

Nadia Passon

Affiliation Dipartimento di Scienze Mediche e Biologiche, Università di Udine, Udine, Italy

Isabella Moroni

Affiliation Department of Child Neurology, Fondazione Istituto Neurologico Besta, Milan, Italy

Graziella Uziel

Affiliation Department of Child Neurology, Fondazione Istituto Neurologico Besta, Milan, Italy

Antonella Pettinari

Affiliation Laboratorio di Genetica Medica, Clinica Pediatrica, Ospedali Riuniti Ancona, Ancona, Italy

Franco Stanzial

Affiliation Servizio di Consulenza Genetica, Centro Provinciale di Coordinamento della Rete delle Malattie Rare, Azienda Sanitaria dell’Alto-Adige, Bolzano, Italy

Raquel Dodelson de Kremer

Affiliation Centro de Estudio de las Metabolopatias Congénitas, CEMECO, University of Córdoba, Córdoba, Argentine

Nydia Beatriz Azar

Affiliation Centro de Estudio de las Metabolopatias Congénitas, CEMECO, University of Córdoba, Córdoba, Argentine

Filiz Hazan

Affiliation Medical Faculty, Genetic Department, Izmir, Turkey

Mirella Filocamo

Affiliation U.O.S.D. Laboratorio Diagnosi Pre-Postnatale Malattie Metaboliche, Istituto G. Gaslini, Genova, Italy

Bruno Bembi

Affiliation Regional Coordinator Center for Rare Diseases, University Hospital Santa Maria della Misericordia, Udine, Italy

Andrea Dardis

dardis.andrea@aoud.sanita.fvg.it

Affiliation Regional Coordinator Center for Rare Diseases, University Hospital Santa Maria della Misericordia, Udine, Italy

Competing Interests

The authors have declared that no competing interests exist.

Author Contributions

Conceived and designed the experiments: AD SZ. Performed the experiments: SZ SC AMOR NBA CML. Analyzed the data: AD MF IM GU BB. Contributed reagents/materials/analysis tools: NP AP FS RDK FH. Wrote the paper: AD BB MF. Performed the 3D structural analysis: CR.