Table 1.
Patient characteristics at first NSAA assessment.
Table 2.
Estimates of MCID for NSAA (raw score) and 6MWD based on distribution methods.
Table 3.
Estimates of MCID for NSAA (linearized scale) based on distribution methods.
Fig 1.
Scatter plot of annual changes in 6MWD vs NSAA total score (non-overlapping changes).
Table 4.
Patient (boys with DMD) characteristics and perceived mobility status.
Fig 2.
Distribution of participant responses for significant change as minimum number of items on NSAA for preventing loss of activity (i.e., preventing a change in score from 1 to 0). The x-axis represents minimum number of sub items for which prevention of loss of function was meaningful for a parent (red) and for a patient with DMD (blue).
Fig 3.
Distribution of participant responses for significant change as minimum number of items on NSAA for maintenance of function (i.e., preventing a change in score from 2 to 1). The x-axis represents minimum number of sub items for which maintaining the activity was meaningful for a parent (red) and for a patient with DMD (blue).
Fig 4.
Participant responses for minimum requirements for participating in a clinical trial lasting 2 years based on improvement of motor function, slowing the decline of motor function, or stopping the decline of motor function of items in the NSAA.
NA = missing response.