Table 1.
Summary of Paroxysmal Nocturnal Hemoglobinuria Patient Preference Questionnaire© content* [15].
Table 2.
Characteristics of the study population.
Fig 1.
Overall treatment preference (N = 95).
Fig 2.
Factors driving patients’ treatment preferencea,b (N = 95).
aPreference response was defined as responding “Strongly” or “Somewhat” prefer respective drug. b1 missing response for “controlling symptoms other than fatigue” and “being able to plan activities” and “effectiveness of the medication until the next infusion; 2 missing responses for “your overall quality of life”.
Fig 3.
Patients’ most important factor for deciding medication preference (N = 95).
The number of patients selecting each preference is at top of bar. aParticipants selecting “Other” were prompted to provide details.
Table 3.
Impact of treatment on measures of patient health-related quality of life.