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Open Access
Peer-reviewed
Research Article
Adeno-associated vector corneal gene therapy reverses corneal clouding in a feline model of mucopolysaccharidosis VI
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Brian C. Gilger,
Roles Conceptualization, Data curation, Formal analysis, Funding acquisition, Writing – review & editing
Affiliation Clinical Sciences, North Carolina State University, Raleigh, North Carolina, United States of America
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Liujiang Song,
Roles Data curation, Writing – review & editing
Affiliations Department of Ophthalmology, University of North Carolina at Chapel Hill, North Carolina, United States of America, Carolina Eye Research Institute, University of North Carolina at Chapel Hill, North Carolina, United States of America, Center for Molecular Medicine, University of North Carolina at Chapel Hill, North Carolina, United States of America
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Tomoko Hasegawa,
Roles Formal analysis, Validation, Writing – original draft, Writing – review & editing
Affiliations Department of Ophthalmology, University of North Carolina at Chapel Hill, North Carolina, United States of America, Carolina Eye Research Institute, University of North Carolina at Chapel Hill, North Carolina, United States of America, Center for Molecular Medicine, University of North Carolina at Chapel Hill, North Carolina, United States of America
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Jacklyn H. Salmon,
Roles Data curation, Writing – review & editing
Affiliation Clinical Sciences, North Carolina State University, Raleigh, North Carolina, United States of America
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Jacquelyn J. Bower,
Roles Data curation, Writing – review & editing
Affiliations Department of Ophthalmology, University of North Carolina at Chapel Hill, North Carolina, United States of America, Carolina Eye Research Institute, University of North Carolina at Chapel Hill, North Carolina, United States of America, Lineberger Comprehensive Cancer Center, University of North Carolina at Chapel Hill, North Carolina, United States of America
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Naveen Vridhachalam,
Roles Data curation, Writing – review & editing
Affiliations Department of Ophthalmology, University of North Carolina at Chapel Hill, North Carolina, United States of America, Carolina Eye Research Institute, University of North Carolina at Chapel Hill, North Carolina, United States of America, Center for Molecular Medicine, University of North Carolina at Chapel Hill, North Carolina, United States of America
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Elisabeth Collins,
Roles Data curation, Writing – review & editing
Affiliation Clinical Sciences, North Carolina State University, Raleigh, North Carolina, United States of America
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Darby Roberts,
Roles Data curation, Writing – review & editing
Affiliation Clinical Sciences, North Carolina State University, Raleigh, North Carolina, United States of America
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Jessica Bagel,
Roles Data curation, Writing – review & editing
Affiliation Department of Referral Center for Animals Models, University of Pennsylvania, Philadelphia, Pennsylvania, United States of America
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Caitlyn Molony,
Roles Data curation, Writing – review & editing
Affiliation Department of Pathobiology, University of Pennsylvania, Philadelphia, Pennsylvania, United States of America
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Charles Vite,
Roles Data curation, Funding acquisition, Writing – review & editing
Affiliation Department of Small Animal Clinical Sciences, College of Veterinary Medicine, University of Florida, Gainesville, Florida, United States of America
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Matthew L. Hirsch
Roles Conceptualization, Data curation, Formal analysis, Funding acquisition, Investigation, Methodology, Resources, Supervision, Writing – original draft, Writing – review & editing
* E-mail: mhirsch@email.unc.edu
Affiliations Department of Ophthalmology, University of North Carolina at Chapel Hill, North Carolina, United States of America, Carolina Eye Research Institute, University of North Carolina at Chapel Hill, North Carolina, United States of America, Center for Molecular Medicine, University of North Carolina at Chapel Hill, North Carolina, United States of America
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Adeno-associated vector corneal gene therapy reverses corneal clouding in a feline model of mucopolysaccharidosis VI
- Brian C. Gilger,
- Liujiang Song,
- Tomoko Hasegawa,
- Jacklyn H. Salmon,
- Jacquelyn J. Bower,
- Naveen Vridhachalam,
- Elisabeth Collins,
- Darby Roberts,
- Jessica Bagel,
- Caitlyn Molony
- Published: December 5, 2025
- https://doi.org/10.1371/journal.pone.0338370