Predicting trajectories of the north star ambulatory assessment total score in Duchenne muscular dystrophy

• Francesco Muntoni,

  Roles Conceptualization, Investigation, Methodology, Supervision, Validation, Writing – original draft, Writing – review & editing

  Affiliation Dubowitz Neuromuscular Centre, NIHR Great Ormond Street Hospital Biomedical Research Centre, Great Ormond Street Institute of Child Health, University College London, & Great Ormond Street Hospital Trust, London, United Kingdom

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• James Signorovitch ,

  Roles Conceptualization, Data curation, Funding acquisition, Investigation, Methodology, Project administration, Resources, Software, Supervision, Validation, Visualization, Writing – original draft, Writing – review & editing

  * E-mail: James.Signorovitch@analysisgroup.com

  Affiliations Analysis Group, Boston, Massachusetts, United States of America, The collaborative Trajectory Analysis Project, Cambridge, Massachusetts, United States of America

  https://orcid.org/0000-0002-4067-8962

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• Nathalie Goemans,

  Roles Conceptualization, Investigation, Supervision, Validation, Writing – review & editing

  Affiliation Child Neurology, University Hospitals Leuven, Leuven, Belgium

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• Adnan Y. Manzur,

  Roles Investigation, Validation, Visualization, Writing – review & editing

  Affiliation Dubowitz Neuromuscular Centre, NIHR Great Ormond Street Hospital Biomedical Research Centre, Great Ormond Street Institute of Child Health, University College London, & Great Ormond Street Hospital Trust, London, United Kingdom

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• Nicolae Done,

  Roles Data curation, Formal analysis, Investigation, Methodology, Software, Supervision, Validation, Visualization, Writing – original draft, Writing – review & editing

  Affiliation Analysis Group, Boston, Massachusetts, United States of America

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• Gautam Sajeev,

  Roles Data curation, Investigation, Methodology, Software, Validation, Visualization, Writing – review & editing

  Affiliation Analysis Group, Boston, Massachusetts, United States of America

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• Jiayang Li,

  Roles Data curation, Formal analysis, Investigation, Methodology, Software, Validation, Visualization, Writing – review & editing

  Affiliation Analysis Group, Boston, Massachusetts, United States of America

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• Hanane Akbarnejad,

  Roles Data curation, Formal analysis, Investigation, Software, Visualization, Writing – review & editing

  Affiliation Analysis Group, Boston, Massachusetts, United States of America

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• Aarushi Sharma,

  Roles Data curation, Formal analysis, Investigation, Software, Visualization, Writing – review & editing

  Affiliation Analysis Group, Boston, Massachusetts, United States of America

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• Susan J. Ward,

  Roles Conceptualization, Funding acquisition, Project administration, Supervision, Validation, Visualization, Writing – original draft, Writing – review & editing

  Affiliation The collaborative Trajectory Analysis Project, Cambridge, Massachusetts, United States of America

  https://orcid.org/0000-0002-5729-5263

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• Erik H. Niks,

  Roles Investigation, Resources, Writing – review & editing

  Affiliation Department of Neurology, Leiden University Medical Center, Leiden, Belgium

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• Laurant Servais,

  Roles Investigation, Resources, Writing – review & editing

  Affiliation Division of Child Neurology, Department of Pediatrics, Centre de Référence des Maladies Neuromusculaires, University Hospital Liège and University of Liège, Liège, Belgium & Department of Paediatrics, MDUK Oxford Neuromuscular Centre & NIHR Oxford Biomedical Research Centre, University of Oxford, Oxford, United Kingdom

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• Eugenio Mercuri,

  Roles Conceptualization, Investigation, Resources, Supervision, Writing – review & editing

  Affiliations Paediatric Neurology, Catholic University, Rome, Italy, Centro Clinico Nemo, Policlinico Gemelli, Fondazione Policlinico Universitario Agostino Gemelli, IRCCS, Rome, Italy

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• Michela Guglieri,

  Roles Investigation, Resources, Writing – review & editing

  Affiliation The John Walton Muscular Dystrophy Research Centre, NIHR Newcastle Biomedical Research Centre, Newcastle University and Newcastle Hospitals NHS Foundation Trust, Newcastle upon Tyne, United Kingdom

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• Volker Straub,

  Roles Conceptualization, Investigation, Resources, Supervision, Writing – review & editing

  Affiliation The John Walton Muscular Dystrophy Research Centre, NIHR Newcastle Biomedical Research Centre, Newcastle University and Newcastle Hospitals NHS Foundation Trust, Newcastle upon Tyne, United Kingdom

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• Imelda de Groot,

  Roles Investigation, Resources, Writing – review & editing

  Affiliation Academic Medical Center Amsterdam, Rehabilitation Center De Trappenberg in Huizen and Radboud University Medical Center, Nijmegen, Netherlands

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• Deborah Ridout,

  Roles Formal analysis, Methodology, Validation, Writing – review & editing

  Affiliation Population Policy and Practice Research and Teaching Department, UCL Great Ormond Street Institute of Child Health, London, United Kingdom

  https://orcid.org/0000-0003-1336-6450

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• PRO-DMD-01 study investigators,

  Affiliation Dubowitz Neuromuscular Centre, NIHR Great Ormond Street Hospital Biomedical Research Centre, Great Ormond Street Institute of Child Health, University College London, & Great Ormond Street Hospital Trust, London, United Kingdom

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• Association Française contre les Myopathies,

  Affiliation Dubowitz Neuromuscular Centre, NIHR Great Ormond Street Hospital Biomedical Research Centre, Great Ormond Street Institute of Child Health, University College London, & Great Ormond Street Hospital Trust, London, United Kingdom

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• The NorthStar Clinical Network,

  Affiliation Dubowitz Neuromuscular Centre, NIHR Great Ormond Street Hospital Biomedical Research Centre, Great Ormond Street Institute of Child Health, University College London, & Great Ormond Street Hospital Trust, London, United Kingdom

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•  [ ... ],
• Craig McDonald

  Roles Conceptualization, Investigation, Resources, Supervision, Writing – review & editing

  Affiliation Department of Physical Medicine and RehabilitationPediatrics, University of California Davis, Sacramento, California, United States of America

  https://orcid.org/0000-0002-8779-3220

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