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Open Access
Peer-reviewed
Research Article
The histone deacetylase inhibitor CT-101 flips the switch to fetal hemoglobin expression in sickle cell disease mice
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Mayuko Takezaki ,
Roles Data curation, Methodology, Writing – original draft
¶‡ MT and BL are co-first authors on this work. LHJ and BSP are co-senior authors on this work.
Affiliation Department of Pediatrics, Georgia Cancer Center, Augusta University, Augusta, Georgia,
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Biaoru Li ,
Roles Data curation, Methodology, Writing – review & editing
¶‡ MT and BL are co-first authors on this work. LHJ and BSP are co-senior authors on this work.
Affiliation Department of Pediatrics, Georgia Cancer Center, Augusta University, Augusta, Georgia,
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Hongyan Xu,
Roles Data curation, Formal analysis, Methodology, Writing – review & editing
Affiliation Department of Biostatistics, Data Science and Epidemiology, Augusta University, Augusta, Georgia,
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Nikhil Patel,
Roles Formal analysis, Methodology, Writing – review & editing
Affiliation Department of Pathology and Laboratory Medicine, Medical College of Georgia at Augusta University, Augusta, Georgia,
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Rudolf Lucas,
Roles Formal analysis, Methodology, Writing – original draft
Affiliation Vascular Biology Center, Department of Pharmacology and Toxicology, Division of Pulmonary and Critical Care Medicine, Medical College of Georgia at Augusta University, Augusta, Georgia,
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Ryan E. Cerbone,
Roles Conceptualization, Methodology, Validation, Writing – review & editing
Affiliations Cetya Therapeutics, Fort Collins, Colorado,, Colorado State University, Department of Chemistry, Fort Collins, Colorado
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Sivanagireddy Koti,
Roles Formal analysis, Methodology, Writing – review & editing
Affiliation Cetya Therapeutics, Fort Collins, Colorado,
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Clifford L. Hendrick,
Roles Conceptualization, Data curation, Funding acquisition, Resources, Writing – original draft
Affiliation Cetya Therapeutics, Fort Collins, Colorado,
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Louis H. Junker ,
Roles Conceptualization, Funding acquisition, Methodology, Resources, Writing – original draft
* E-mail: ljunker@cetya-therapeutics.com (LHJ); bpace@augusta.edu (BSP)
¶‡ MT and BL are co-first authors on this work. LHJ and BSP are co-senior authors on this work.
Affiliation Cetya Therapeutics, Fort Collins, Colorado,
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Betty S. Pace
Roles Conceptualization, Data curation, Funding acquisition, Methodology, Project administration, Resources, Writing – review & editing
* E-mail: ljunker@cetya-therapeutics.com (LHJ); bpace@augusta.edu (BSP)
¶‡ MT and BL are co-first authors on this work. LHJ and BSP are co-senior authors on this work.
Affiliation Department of Pediatrics, Georgia Cancer Center, Augusta University, Augusta, Georgia,
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The histone deacetylase inhibitor CT-101 flips the switch to fetal hemoglobin expression in sickle cell disease mice
- Mayuko Takezaki,
- Biaoru Li,
- Hongyan Xu,
- Nikhil Patel,
- Rudolf Lucas,
- Ryan E. Cerbone,
- Sivanagireddy Koti,
- Clifford L. Hendrick,
- Louis H. Junker,
- Betty S. Pace
- Published: May 13, 2025
- https://doi.org/10.1371/journal.pone.0323550