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Gene delivery of AGAT and GAMT boosts creatine levels in creatine transporter deficiency patient fibroblasts
- Chloe Wells,
- Jon Sorgenfrei,
- Sadie L. Johnson,
- Devin Albertson,
- Jared Rutter,
- Steven Andrew Baker
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- Published: May 8, 2025
- https://doi.org/10.1371/journal.pone.0319350