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Study Protocol
Evaluating elexacaftor/tezacaftor/ivacaftor (ETI; Trikafta™) for treatment of patients with non-cystic fibrosis bronchiectasis (NCFBE): A clinical study protocol
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Colin E. Swenson ,
Contributed equally to this work with: Colin E. Swenson, William R. Hunt
Roles Conceptualization, Formal analysis, Investigation, Methodology, Project administration, Resources, Supervision, Writing – original draft, Writing – review & editing
Affiliation Division of Pulmonology, Allergy, Critical Care and Sleep Medicine, Department of Medicine, Emory University School of Medicine, Atlanta, GA, United States of America
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William R. Hunt ,
Contributed equally to this work with: Colin E. Swenson, William R. Hunt
Roles Conceptualization, Formal analysis, Investigation, Methodology, Project administration, Resources, Writing – original draft, Writing – review & editing
Affiliation Division of Pulmonology, Allergy, Critical Care and Sleep Medicine, Department of Medicine, Emory University School of Medicine, Atlanta, GA, United States of America
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Candela Manfredi,
Roles Conceptualization, Formal analysis, Investigation, Methodology, Project administration, Resources, Writing – review & editing
Affiliation Division of Pulmonary, Asthma, Cystic Fibrosis and Sleep, Department of Pediatrics, Emory University School of Medicine and Children’s Healthcare of Atlanta, Atlanta, GA, United States of America
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Diana J. Beltran,
Roles Formal analysis, Investigation, Methodology, Project administration, Resources, Writing – review & editing
Affiliation Georgia Clinical & Translational Science Alliance, Emory University, Atlanta, GA, United States of America
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Jeong S. Hong,
Roles Conceptualization, Investigation, Writing – review & editing
Affiliation Division of Pulmonary, Asthma, Cystic Fibrosis and Sleep, Department of Pediatrics, Emory University School of Medicine and Children’s Healthcare of Atlanta, Atlanta, GA, United States of America
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Brian R. Davis,
Roles Formal analysis, Investigation, Methodology, Supervision, Writing – review & editing
Affiliation Division of Pulmonary, Allergy & Critical Care Medicine, University of Alabama at Birmingham Heersink School of Medicine, Birmingham, AL, United States of America
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Shingo Suzuki,
Roles Formal analysis, Investigation, Methodology, Writing – review & editing
Affiliation Division of Pulmonary, Allergy & Critical Care Medicine, University of Alabama at Birmingham Heersink School of Medicine, Birmingham, AL, United States of America
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Cristina Barillá,
Roles Formal analysis, Investigation, Writing – review & editing
Affiliation Division of Pulmonary, Allergy & Critical Care Medicine, University of Alabama at Birmingham Heersink School of Medicine, Birmingham, AL, United States of America
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Andras Rab,
Roles Conceptualization, Investigation, Methodology, Writing – review & editing
Affiliation Division of Pulmonary, Asthma, Cystic Fibrosis and Sleep, Department of Pediatrics, Emory University School of Medicine and Children’s Healthcare of Atlanta, Atlanta, GA, United States of America
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Cynthia Chico,
Roles Formal analysis, Investigation, Writing – review & editing
Affiliation Georgia Clinical & Translational Science Alliance, Emory University, Atlanta, GA, United States of America
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Joy Dangerfield,
Roles Formal analysis, Investigation, Writing – review & editing
Affiliation Division of Pulmonary, Asthma, Cystic Fibrosis and Sleep, Department of Pediatrics, Emory University School of Medicine and Children’s Healthcare of Atlanta, Atlanta, GA, United States of America
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Ashleigh Streby,
Roles Formal analysis, Supervision, Writing – review & editing
Affiliation Division of Pulmonary, Asthma, Cystic Fibrosis and Sleep, Department of Pediatrics, Emory University School of Medicine and Children’s Healthcare of Atlanta, Atlanta, GA, United States of America
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Erin Barton,
Roles Investigation, Supervision
Affiliation Division of Pulmonology, Allergy, Critical Care and Sleep Medicine, Department of Medicine, Emory University School of Medicine, Atlanta, GA, United States of America
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Elizabeth M. Cox,
Roles Formal analysis, Investigation, Writing – review & editing
Affiliation Division of Pulmonology, Allergy, Critical Care and Sleep Medicine, Department of Medicine, Emory University School of Medicine, Atlanta, GA, United States of America
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Arlene A. Stecenko,
Roles Conceptualization, Writing – review & editing
Affiliation Division of Pulmonary, Asthma, Cystic Fibrosis and Sleep, Department of Pediatrics, Emory University School of Medicine and Children’s Healthcare of Atlanta, Atlanta, GA, United States of America
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Adrianna Westbrook,
Roles Formal analysis, Writing – review & editing
Affiliation Division of Pulmonary, Asthma, Cystic Fibrosis and Sleep, Department of Pediatrics, Emory University School of Medicine and Children’s Healthcare of Atlanta, Atlanta, GA, United States of America
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Rebecca Kapolka,
Roles Conceptualization, Investigation, Project administration, Resources, Writing – original draft, Writing – review & editing
Affiliation Division of Pulmonology, Allergy, Critical Care and Sleep Medicine, Department of Medicine, Emory University School of Medicine, Atlanta, GA, United States of America
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Eric J. Sorscher
Roles Conceptualization, Formal analysis, Funding acquisition, Investigation, Methodology, Project administration, Resources, Supervision, Writing – original draft, Writing – review & editing
* E-mail: esorscher@emory.edu
Affiliation Division of Pulmonary, Asthma, Cystic Fibrosis and Sleep, Department of Pediatrics, Emory University School of Medicine and Children’s Healthcare of Atlanta, Atlanta, GA, United States of America
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Evaluating elexacaftor/tezacaftor/ivacaftor (ETI; Trikafta™) for treatment of patients with non-cystic fibrosis bronchiectasis (NCFBE): A clinical study protocol
- Colin E. Swenson,
- William R. Hunt,
- Candela Manfredi,
- Diana J. Beltran,
- Jeong S. Hong,
- Brian R. Davis,
- Shingo Suzuki,
- Cristina Barillá,
- Andras Rab,
- Cynthia Chico
- Published: February 14, 2025
- https://doi.org/10.1371/journal.pone.0316721