Association between under-dose of enzyme replacement therapy and quality of life in adults with late-onset Pompe disease in China: A retrospective matched cohort study

• Huanyu Zhang ,

  Contributed equally to this work with: Huanyu Zhang, Shanquan Chen

  Roles Conceptualization, Formal analysis, Investigation, Methodology, Project administration, Writing – original draft, Writing – review & editing

  Affiliations Shenzhen Research Institute, The Chinese University of Hong Kong, Shenzhen, China, Clinical Big Data Research Center, The Seventh Affiliated Hospital, Sun Yat-sen University, Shenzhen, China

  https://orcid.org/0000-0001-6480-2510

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• Shanquan Chen ,

  Contributed equally to this work with: Huanyu Zhang, Shanquan Chen

  Roles Conceptualization, Methodology, Writing – original draft, Writing – review & editing

  Affiliation International Centre for Evidence in Disability, London School of Hygiene & Tropical Medicine, London, United Kingdom

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• Richard Huan Xu,

  Roles Conceptualization, Methodology, Writing – review & editing

  Affiliation Department of Rehabilitation Sciences, The Hong Kong Polytechnic University, Hong Kong SAR, China

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• Siyue Yu,

  Roles Investigation, Project administration, Writing – review & editing

  Affiliation Faculty of Medicine, Jockey Club School of Public Health and Primary Care, The Chinese University of Hong Kong, Hong Kong SAR, China

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• Jiazhou Yu,

  Roles Writing – review & editing

  Affiliation Faculty of Medicine, Jockey Club School of Public Health and Primary Care, The Chinese University of Hong Kong, Hong Kong SAR, China

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• Dong Dong

  Roles Conceptualization, Project administration, Supervision, Writing – original draft, Writing – review & editing

  * E-mail: dongdong@cuhk.edu.hk

  Affiliations Shenzhen Research Institute, The Chinese University of Hong Kong, Shenzhen, China, Faculty of Medicine, Jockey Club School of Public Health and Primary Care, The Chinese University of Hong Kong, Hong Kong SAR, China

  https://orcid.org/0000-0001-9784-6472

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