Characterization of patients with Duchenne muscular dystrophy across previously developed health states

• Francesco Muntoni,

  Roles Conceptualization, Methodology, Writing – review & editing

  Affiliation Dubowitz Neuromuscular Centre, Great Ormond Street Institute of Child Health, London, United Kingdom

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• Nathalie Goemans,

  Roles Investigation, Writing – review & editing

  Affiliation University Hospitals Leuven, Child Neurology, Leuven, Belgium

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• Nate Posner,

  Roles Conceptualization, Funding acquisition, Methodology, Project administration, Resources, Supervision, Writing – review & editing

  Affiliation Pfizer, Inc., New York, NY, United States of America

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• James Signorovitch ,

  Roles Conceptualization, Data curation, Formal analysis, Funding acquisition, Methodology, Project administration, Resources, Software, Supervision, Validation, Visualization, Writing – original draft, Writing – review & editing

  * E-mail: James.Signorovitch@analysisgroup.com

  Affiliations Analysis Group, Inc., Boston, MA, United States of America, collaborative Trajectory Analysis Project (cTAP), Cambridge, MA, United States of America

  https://orcid.org/0000-0002-4067-8962

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• Michaela Johnson,

  Roles Data curation, Formal analysis, Methodology, Project administration, Resources, Software, Supervision, Validation, Visualization, Writing – original draft, Writing – review & editing

  Affiliation Analysis Group, Inc., Boston, MA, United States of America

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• Chujun He,

  Roles Data curation, Formal analysis, Software, Validation, Visualization, Writing – review & editing

  Affiliation Analysis Group, Inc., Boston, MA, United States of America

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• Patricia Dorling,

  Roles Conceptualization, Writing – review & editing

  Affiliation Chiesi USA, Inc. Boston, MA, United States of America

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• Katherine Beaverson,

  Roles Conceptualization, Writing – review & editing

  Affiliation Pfizer, Inc., New York, NY, United States of America

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• Jose Alvir,

  Roles Writing – review & editing

  Affiliation Pfizer, Inc., New York, NY, United States of America

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• Matthias Mahn,

  Roles Writing – review & editing

  Affiliation Pfizer, Inc., New York, NY, United States of America

  https://orcid.org/0000-0002-1629-9372

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• Susan J. Ward,

  Roles Conceptualization, Funding acquisition, Methodology, Project administration, Resources, Supervision, Writing – review & editing

  Affiliation collaborative Trajectory Analysis Project (cTAP), Cambridge, MA, United States of America

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• Craig M. McDonald,

  Roles Investigation, Writing – review & editing

  Affiliation Department of Physical Medicine and Rehabilitation, University of California, Davis, Sacramento, CA, United States of America

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• Eugenio Mercuri,

  Roles Investigation, Writing – review & editing

  Affiliations Pediatric Neurology, Catholic University, Rome, Italy, Centro Clinico NeMO, Fondazione Policlinico Gemelli IRCCS, Rome, Italy

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• the PRO-DMD-01 study, the Imaging DMD study, iMDEX, the collaborative Trajectory Analysis Project (cTAP)

  ¶Membership of the PRO-DMD-01 study, the Imaging DMD study, iMDEX, and the collaborative Trajectory Analysis Project (cTAP) is listed in the Acknowledgments.

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