Meaningful changes in motor function in Duchenne muscular dystrophy (DMD): A multi-center study

• Francesco Muntoni,

  Roles Conceptualization, Investigation, Resources, Writing – original draft, Writing – review & editing

  Affiliation Dubowitz Neuromuscular Centre, NIHR Great Ormond Street Hospital Biomedical Research Centre, Great Ormond Street Institute of Child Health, University College London, & Great Ormond Street Hospital Trust, London, United Kingdom

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• James Signorovitch ,

  Roles Conceptualization, Data curation, Formal analysis, Funding acquisition, Methodology, Project administration, Software, Supervision, Validation, Visualization, Writing – original draft, Writing – review & editing

  * E-mail: James.signorovitch@analysisgroup.com

  Affiliations Analysis Group, Inc., Boston, Massachusetts, United States of America, The collaborative Trajectory Analysis Project, Cambridge, Massachusetts, United States of America

  https://orcid.org/0000-0002-4067-8962

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• Gautam Sajeev,

  Roles Data curation, Formal analysis, Methodology, Project administration, Software, Supervision, Validation, Visualization, Writing – original draft, Writing – review & editing

  Affiliation Analysis Group, Inc., Boston, Massachusetts, United States of America

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• Nicolae Done,

  Roles Data curation, Formal analysis, Methodology, Project administration, Software, Supervision, Validation, Visualization, Writing – review & editing

  Affiliation Analysis Group, Inc., Boston, Massachusetts, United States of America

  https://orcid.org/0000-0001-6517-646X

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• Zhiwen Yao,

  Roles Data curation, Formal analysis, Software, Validation, Visualization, Writing – review & editing

  Affiliation Analysis Group, Inc., Boston, Massachusetts, United States of America

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• Nathalie Goemans,

  Roles Investigation, Resources, Writing – review & editing

  Affiliation Child Neurology, University Hospitals Leuven, Leuven, Belgium

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• Craig McDonald,

  Roles Investigation, Resources, Writing – review & editing

  Affiliation Department of Physical Medicine and Rehabilitation and Pediatrics, University of California, Davis, Sacramento, California, United States of America

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• Eugenio Mercuri,

  Roles Investigation, Resources, Writing – review & editing

  Affiliation Department of Pediatric Neurology, Fondazione Policlinico Gemelli IRCCS, Catholic University, Rome, Italy

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• Erik H. Niks,

  Roles Investigation, Resources, Writing – review & editing

  Affiliation Department of Neurology, Leiden University Medical Centre, Leiden, Netherlands

  https://orcid.org/0000-0001-5892-5143

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• Brenda Wong,

  Roles Investigation, Resources, Writing – review & editing

  Affiliation Department of Pediatrics, University of Massachusetts Medical School, Worcester, Massachusetts, United States of America

  https://orcid.org/0000-0002-0971-9789

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• Krista Vandenborne,

  Roles Investigation, Resources, Writing – review & editing

  Affiliation Department of Physical Therapy, University of Florida, Gainesville, Florida, United States of America

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• Volker Straub,

  Roles Investigation, Resources, Writing – review & editing

  Affiliation John Walton Muscular Dystrophy Research Centre, Newcastle University and Newcastle Hospitals NHS Foundation Trust, Newcastle upon Tyne, United Kingdom

  https://orcid.org/0000-0001-9046-3540

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• Imelda J. M. de Groot,

  Roles Investigation, Resources, Writing – review & editing

  Affiliation Department of Rehabilitation, Donders Centre of Neuroscience, Radboud University Nijmegen Medical Center, Nijmegen, Netherlands

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• Cuixia Tian,

  Roles Investigation, Resources, Writing – review & editing

  Affiliation Cincinnati Children’s Hospital Medical Center, Cincinnati, Ohio & College of Medicine, University of Cincinnati, Cincinnati, Ohio, United States of America

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• Adnan Manzur,

  Roles Investigation, Resources, Writing – review & editing

  Affiliation Dubowitz Neuromuscular Centre, NIHR Great Ormond Street Hospital Biomedical Research Centre, Great Ormond Street Institute of Child Health, University College London, & Great Ormond Street Hospital Trust, London, United Kingdom

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• Ibrahima Dieye,

  Roles Data curation, Formal analysis, Software, Validation, Visualization, Writing – review & editing

  Affiliation Analysis Group, Inc., Boston, Massachusetts, United States of America

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• Henry Lane,

  Roles Data curation, Formal analysis, Software, Validation, Visualization, Writing – review & editing

  Affiliation Analysis Group, Inc., Boston, Massachusetts, United States of America

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• Susan J. Ward,

  Roles Conceptualization, Funding acquisition, Project administration, Supervision, Writing – review & editing

  Affiliation The collaborative Trajectory Analysis Project, Cambridge, Massachusetts, United States of America

  https://orcid.org/0000-0002-5729-5263

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• Laurent Servais,

  Roles Investigation, Resources, Writing – review & editing

  Affiliations Department of Paediatrics, MDUK Oxford Neuromuscular Center, University of Oxford, Oxford, United Kingdom, Neuromuscular Center of Liège, Division of Paediatrics, CHU and University of Liège, Liège, Belgium

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• PRO-DMD-01 study investigators ,

  ¶Memberships are provided in the Acknowledgments

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• Association Française contre les Myopathies ,

  ¶Memberships are provided in the Acknowledgments

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• The UK NorthStar Clinical Network ,

  ¶Memberships are provided in the Acknowledgments

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• ImagingDMD investigators ,

  ¶Memberships are provided in the Acknowledgments

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•  [ ... ],
• cTAP

  ¶Memberships are provided in the Acknowledgments

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