Application of observational research methods to real-world studies for rare disease drugs: A scoping review protocol

• Yuti P. Patel ,

  Contributed equally to this work with: Yuti P. Patel

  Roles Conceptualization, Data curation, Formal analysis, Funding acquisition, Investigation, Methodology, Project administration, Resources, Software, Writing – original draft, Writing – review & editing

  Affiliation Leslie Dan Faculty of Pharmacy, University of Toronto, Toronto, Ontario, Canada

  https://orcid.org/0009-0004-4879-4441

  ⨯
• Lea Ghaddar ,

  Roles Formal analysis, Validation, Writing – review & editing

  ¶‡ LG, YL and NK also contributed equally to this work.

  Affiliation Leslie Dan Faculty of Pharmacy, University of Toronto, Toronto, Ontario, Canada

  ⨯
• Yuqi Lin ,

  Roles Formal analysis, Validation, Writing – review & editing

  ¶‡ LG, YL and NK also contributed equally to this work.

  Affiliation Leslie Dan Faculty of Pharmacy, University of Toronto, Toronto, Ontario, Canada

  ⨯
• Nuzat Karim ,

  Roles Formal analysis, Validation, Writing – review & editing

  ¶‡ LG, YL and NK also contributed equally to this work.

  Affiliation Leslie Dan Faculty of Pharmacy, University of Toronto, Toronto, Ontario, Canada

  ⨯
• Kelvin Chan,

  Roles Conceptualization, Methodology, Supervision, Validation, Writing – review & editing

  Affiliations Sunnybrook Odette Cancer Centre, University of Toronto, Toronto, Ontario, Canada, Division of Biostatistics, Dalla Lana School of Public Health, University of Toronto, Toronto, Ontario, Canada

  ⨯
• Lee Dupuis,

  Roles Conceptualization, Methodology, Supervision, Validation, Writing – review & editing

  Affiliations Leslie Dan Faculty of Pharmacy, University of Toronto, Toronto, Ontario, Canada, The Hospital for Sick Children (SickKids), Toronto, Ontario, Canada

  https://orcid.org/0000-0002-7699-1061

  ⨯
• Mina Tadrous

  Roles Conceptualization, Data curation, Formal analysis, Funding acquisition, Investigation, Methodology, Project administration, Resources, Software, Supervision, Validation, Writing – review & editing

  * E-mail: mina.tadrous@utoronto.ca

  Affiliation Leslie Dan Faculty of Pharmacy, University of Toronto, Toronto, Ontario, Canada

  https://orcid.org/0000-0003-1911-6129

  ⨯