A phase 2 open-label study of the safety and efficacy of weekly dosing of ATL1102 in patients with non-ambulatory Duchenne muscular dystrophy and pharmacology in mdx mice

• Ian R. Woodcock ,

  Roles Data curation, Formal analysis, Methodology, Project administration, Writing – original draft, Writing – review & editing

  * E-mail: ian.woodcock@rch.org.au

  Affiliations Department of Neurology, The Royal Children’s Hospital, Melbourne, Australia, The Murdoch Children’s Research Institute, Melbourne, Australia, Department of Paediatrics, University of Melbourne, Melbourne, Australia

  https://orcid.org/0000-0002-4902-034X

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• George Tachas,

  Roles Conceptualization, Funding acquisition, Methodology, Resources, Writing – original draft, Writing – review & editing

  Affiliation Antisense Therapeutics Ltd, Melbourne, Australia

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• Nuket Desem,

  Roles Formal analysis, Project administration, Writing – review & editing

  Affiliation Antisense Therapeutics Ltd, Melbourne, Australia

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• Peter J. Houweling,

  Roles Conceptualization, Data curation, Methodology, Project administration, Supervision, Writing – original draft, Writing – review & editing

  Affiliations The Murdoch Children’s Research Institute, Melbourne, Australia, Department of Paediatrics, University of Melbourne, Melbourne, Australia

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• Michael Kean,

  Roles Data curation, Software, Writing – review & editing

  Affiliation Department of Medical Imaging, The Royal Children’s Hospital, Melbourne, Australia

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• Jaiman Emmanuel,

  Roles Data curation, Formal analysis, Writing – review & editing

  Affiliation Department of Medical Imaging, The Royal Children’s Hospital, Melbourne, Australia

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• Rachel Kennedy,

  Roles Project administration, Writing – review & editing

  Affiliations Department of Neurology, The Royal Children’s Hospital, Melbourne, Australia, The Murdoch Children’s Research Institute, Melbourne, Australia, Department of Physiotherapy, University of Melbourne, Melbourne, Australia

  https://orcid.org/0000-0003-1805-6937

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• Kate Carroll,

  Roles Project administration, Supervision, Writing – review & editing

  Affiliations Department of Neurology, The Royal Children’s Hospital, Melbourne, Australia, The Murdoch Children’s Research Institute, Melbourne, Australia

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• Katy de Valle,

  Roles Project administration, Writing – review & editing

  Affiliations Department of Neurology, The Royal Children’s Hospital, Melbourne, Australia, The Murdoch Children’s Research Institute, Melbourne, Australia, Department of Physiotherapy, University of Melbourne, Melbourne, Australia

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• Justine Adams,

  Roles Writing – review & editing

  Affiliation The Murdoch Children’s Research Institute, Melbourne, Australia

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• Shireen R. Lamandé,

  Roles Resources, Supervision, Writing – review & editing

  Affiliations The Murdoch Children’s Research Institute, Melbourne, Australia, Department of Paediatrics, University of Melbourne, Melbourne, Australia

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• Chantal Coles,

  Roles Formal analysis, Writing – review & editing

  Affiliation The Murdoch Children’s Research Institute, Melbourne, Australia

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• Chrystal Tiong,

  Roles Formal analysis, Methodology, Writing – review & editing

  Affiliation The Murdoch Children’s Research Institute, Melbourne, Australia

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• Matthew Burton,

  Roles Writing – review & editing

  Affiliation The Murdoch Children’s Research Institute, Melbourne, Australia

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• Daniella Villano,

  Roles Supervision, Writing – review & editing

  Affiliation Department of Neurology, The Royal Children’s Hospital, Melbourne, Australia

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• Peter Button,

  Roles Formal analysis, Software, Writing – review & editing

  Affiliation McCloud Consulting Group, Sydney, Australia

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• Jean-Yves Hogrel,

  Roles Formal analysis, Writing – review & editing

  Affiliation Institut de Myologie, GH Pitié-Salpêtrière, Paris, France

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• Sarah Catling-Seyffer,

  Roles Project administration, Writing – review & editing

  Affiliations Department of Neurology, The Royal Children’s Hospital, Melbourne, Australia, The Murdoch Children’s Research Institute, Melbourne, Australia

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• Monique M. Ryan,

  Roles Conceptualization, Methodology, Supervision, Writing – review & editing

  Affiliations Department of Neurology, The Royal Children’s Hospital, Melbourne, Australia, The Murdoch Children’s Research Institute, Melbourne, Australia, Department of Paediatrics, University of Melbourne, Melbourne, Australia

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• Martin B. Delatycki,

  Roles Supervision, Writing – review & editing

  Affiliations Victorian Clinical Genetics Service, Melbourne, Australia, Murdoch Children’s Research Institute, Bruce Lefroy Centre for Genetic Health Research, Melbourne, Australia

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•  [ ... ],
• Eppie M. Yiu

  Roles Supervision, Writing – original draft, Writing – review & editing

  Affiliations Department of Neurology, The Royal Children’s Hospital, Melbourne, Australia, The Murdoch Children’s Research Institute, Melbourne, Australia, Department of Paediatrics, University of Melbourne, Melbourne, Australia

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