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Open Access
Peer-reviewed
Research Article
AAV2/4-RS1 gene therapy in the retinoschisin knockout mouse model of X-linked retinoschisis
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Brittni A. Scruggs,
Roles Conceptualization, Formal analysis, Investigation, Methodology, Writing – original draft, Writing – review & editing
Current address: Department of Ophthalmology, Mayo Clinic, Rochester, Minnesota, United States of America
Affiliation University of Iowa Institute for Vision Research and the Department of Ophthalmology and Visual Sciences, University of Iowa, Iowa City, Iowa, United States of America
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Sajag Bhattarai,
Roles Conceptualization, Formal analysis, Investigation, Methodology, Writing – review & editing
Affiliation University of Iowa Institute for Vision Research and the Department of Ophthalmology and Visual Sciences, University of Iowa, Iowa City, Iowa, United States of America
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Megan Helms,
Roles Data curation, Formal analysis, Investigation
Current address: Advocate Illinois Masonic Medical Center, Chicago, Illinois, United States of America
Affiliation University of Iowa Institute for Vision Research and the Department of Ophthalmology and Visual Sciences, University of Iowa, Iowa City, Iowa, United States of America
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Ioana Cherascu,
Roles Data curation, Investigation
Affiliation University of Iowa Institute for Vision Research and the Department of Ophthalmology and Visual Sciences, University of Iowa, Iowa City, Iowa, United States of America
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Adisa Salesevic,
Roles Data curation, Investigation
Current address: Integrated DNA Technologies, Coralville, Iowa, United States of America
Affiliation University of Iowa Institute for Vision Research and the Department of Ophthalmology and Visual Sciences, University of Iowa, Iowa City, Iowa, United States of America
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Elliot Stalter,
Roles Data curation, Investigation
Affiliations University of Iowa Institute for Vision Research and the Department of Ophthalmology and Visual Sciences, University of Iowa, Iowa City, Iowa, United States of America, Carver College of Medicine, University of Iowa, Iowa City, Iowa, United States of America
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Joseph Laird,
Roles Data curation, Formal analysis, Methodology
Affiliation Department of Biochemistry, University of Iowa, Iowa City, Iowa, United States of America
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Sheila A. Baker,
Roles Conceptualization, Data curation, Formal analysis, Investigation, Methodology, Writing – review & editing
Affiliations University of Iowa Institute for Vision Research and the Department of Ophthalmology and Visual Sciences, University of Iowa, Iowa City, Iowa, United States of America, Department of Biochemistry, University of Iowa, Iowa City, Iowa, United States of America, Interdisciplinary Graduate Program in Genetics, University of Iowa, Iowa City, Iowa, United States of America
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Arlene V. Drack
Roles Conceptualization, Data curation, Formal analysis, Funding acquisition, Investigation, Methodology, Project administration, Resources, Supervision, Writing – review & editing
* E-mail: arlene-drack@uiowa.edu
Affiliations University of Iowa Institute for Vision Research and the Department of Ophthalmology and Visual Sciences, University of Iowa, Iowa City, Iowa, United States of America, Carver College of Medicine, University of Iowa, Iowa City, Iowa, United States of America, Interdisciplinary Graduate Program in Genetics, University of Iowa, Iowa City, Iowa, United States of America, Department of Pediatrics, University of Iowa, Iowa City, Iowa, United States of America
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AAV2/4-RS1 gene therapy in the retinoschisin knockout mouse model of X-linked retinoschisis
- Brittni A. Scruggs,
- Sajag Bhattarai,
- Megan Helms,
- Ioana Cherascu,
- Adisa Salesevic,
- Elliot Stalter,
- Joseph Laird,
- Sheila A. Baker,
- Arlene V. Drack
- Published: December 7, 2022
- https://doi.org/10.1371/journal.pone.0276298