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Pharmacotherapy alleviates pathological changes in human direct reprogrammed neuronal cell model of myotonic dystrophy type 1
- Mougina K. Eltahir,
- Masayuki Nakamori,
- Satoshi Hattori,
- Takashi Kimura,
- Hideki Mochizuki,
- Seiichi Nagano
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- Published: July 1, 2022
- https://doi.org/10.1371/journal.pone.0269683