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Short-term treatment of golden retriever muscular dystrophy (GRMD) dogs with rAAVrh74.MHCK7.GALGT2 induces muscle glycosylation and utrophin expression but has no significant effect on muscle strength
- Paul T. Martin,
- Deborah A. Zygmunt,
- Anna Ashbrook,
- Sonia Hamilton,
- Davin Packer,
- Sharla M. Birch,
- Amanda K. Bettis,
- Cynthia J. Balog-Alvarez,
- Lee-Jae Guo,
- Peter P. Nghiem
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- Published: March 26, 2021
- https://doi.org/10.1371/journal.pone.0248721