Bayesian modeling and simulation to inform rare disease drug development early decision-making: Application to Duchenne muscular dystrophy

• Janelle L. Lennie ,

  Roles Conceptualization, Data curation, Formal analysis, Investigation, Validation, Visualization, Writing – original draft, Writing – review & editing

  * E-mail: janellelennie@gmail.com

  Affiliations Biomedical Engineering, University of Connecticut, Storrs, Connecticut, United States of America, Metrum Research Group, Tariffville, Connecticut, United States of America

  https://orcid.org/0000-0001-6084-7172

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• John T. Mondick,

  Roles Conceptualization, Methodology, Project administration, Validation, Writing – review & editing

  Affiliation Metrum Research Group, Tariffville, Connecticut, United States of America

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• Marc R. Gastonguay

  Roles Conceptualization, Methodology, Project administration, Supervision, Validation, Writing – review & editing

  Affiliations Biomedical Engineering, University of Connecticut, Storrs, Connecticut, United States of America, Metrum Research Group, Tariffville, Connecticut, United States of America

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