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Open Access
Peer-reviewed
Research Article
Oral cysteamine as an adjunct treatment in cystic fibrosis pulmonary exacerbations: An exploratory randomized clinical trial
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Graham Devereux,
Roles Conceptualization, Formal analysis, Project administration, Supervision, Writing – original draft
Affiliation Liverpool School of Tropical Medicine, Liverpool, United Kingdom
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Danielle Wrolstad,
Roles Data curation, Formal analysis, Writing – review & editing
Affiliation Precision for Medicine, Oncology and Rare Disease, Carlsbad, CA, United States of America
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Stephen J. Bourke,
Roles Data curation, Investigation, Supervision
Affiliation Royal Victoria Infirmary, Newcastle, United Kingdom
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Cori L. Daines,
Roles Data curation, Investigation, Supervision
Affiliation Banner University of Arizona Medical Center, Tucson, Arizona, United States of America
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Simon Doe,
Roles Data curation, Investigation, Supervision
Affiliation Royal Victoria Infirmary, Newcastle, United Kingdom
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Ryan Dougherty,
Roles Data curation, Investigation, Supervision
Affiliation San Francisco Critical Care Medical Group California Pacific Medical Center, San Francisco, United States of America
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Rose Franco,
Roles Data curation, Investigation, Supervision
Affiliation The Medical College of Wisconsin/Froedtert Hospital, Milwaukee, Wisconsin, United States of America
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Alastair Innes,
Roles Data curation, Investigation, Supervision
Affiliation Western General Hospital, Edinburgh, United Kingdom
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Benjamin T. Kopp,
Roles Data curation, Investigation, Supervision
Affiliation Nationwide Children's Hospital, Columbus, OH, United States of America
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Jorge Lascano,
Roles Data curation, Investigation, Supervision
Affiliation University of Florida, Gainesville, Florida, United States of America
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Daniel Layish,
Roles Data curation, Investigation, Supervision
Affiliation Central Florida Pulmonary Group, Orlando, Florida, United States of America
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Gordon MacGregor,
Roles Data curation, Investigation, Supervision
Affiliation Queen Elizabeth University Hospital, Glasgow, United Kingdom
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Lorna Murray,
Roles Data curation, Investigation, Supervision
Affiliation Raigmore Hospital, Inverness, United Kingdom
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Daniel Peckham,
Roles Data curation, Investigation, Supervision, Writing – review & editing
Affiliation St James’s University Hospital, Leeds, United Kingdom
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Vincenzina Lucidi,
Roles Data curation, Investigation, Supervision
Affiliation Ospedale Padiatrico Bambino Gesu Centro Fibrosi Cistica, Rome, Italy
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Emma Lovie,
Roles Data curation, Investigation, Methodology
Affiliation NovaBiotics Ltd, Aberdeen, United Kingdom
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Jennifer Robertson,
Roles Data curation, Investigation, Methodology
Affiliation NovaBiotics Ltd, Aberdeen, United Kingdom
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Douglas J. Fraser-Pitt ,
Roles Conceptualization, Project administration, Supervision, Writing – review & editing
* E-mail: Doug@novabiotics.co.uk
Affiliation NovaBiotics Ltd, Aberdeen, United Kingdom
⨯ - [ ... ],
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Deborah A. O'Neil
Roles Conceptualization, Funding acquisition, Methodology, Project administration, Resources, Supervision, Writing – review & editing
Affiliation NovaBiotics Ltd, Aberdeen, United Kingdom
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Oral cysteamine as an adjunct treatment in cystic fibrosis pulmonary exacerbations: An exploratory randomized clinical trial
- Graham Devereux,
- Danielle Wrolstad,
- Stephen J. Bourke,
- Cori L. Daines,
- Simon Doe,
- Ryan Dougherty,
- Rose Franco,
- Alastair Innes,
- Benjamin T. Kopp,
- Jorge Lascano
- Published: December 28, 2020
- https://doi.org/10.1371/journal.pone.0242945