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Efficacy of pentosan polysulfate in in vitro models of lysosomal storage disorders: Fabry and Gaucher Disease
- Andrea N. Crivaro,
- Juan M. Mucci,
- Constanza M. Bondar,
- Maximiliano E. Ormazabal,
- Romina Ceci,
- Calogera Simonaro,
- Paula A. Rozenfeld
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- Published: May 31, 2019
- https://doi.org/10.1371/journal.pone.0217780