Defining consensus opinion to develop randomised controlled trials in rare diseases using Bayesian design: An example of a proposed trial of adalimumab versus pamidronate for children with CNO/CRMO

• A. V. Ramanan ,

  Roles Conceptualization, Data curation, Funding acquisition, Investigation, Methodology, Writing – original draft, Writing – review & editing

  * E-mail: avramanan@hotmail.com

  Affiliation Paediatric Rheumatology, Bristol Royal Hospital for Children, Bristol and Bristol Medical School, University of Bristol, Bristol, United Kingdom

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• L. V. Hampson,

  Roles Conceptualization, Data curation, Formal analysis, Funding acquisition, Investigation, Methodology, Software, Validation, Writing – original draft, Writing – review & editing

  Affiliation Statistical Methodology and Consulting, Novartis Pharma AG, Basel, Switzerland

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• H Lythgoe,

  Roles Data curation, Formal analysis, Investigation

  Affiliations Department of Women's & Children's Health, Institute of Translational Medicine, University of Liverpool, Liverpool, United Kingdom, Department of Paediatric Rheumatology, Alder Hey Children’s NHS Foundation Trust, Liverpool, United Kingdom

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• A. P. Jones,

  Roles Conceptualization, Data curation, Formal analysis, Funding acquisition, Investigation, Methodology, Project administration, Resources, Writing – original draft, Writing – review & editing

  Affiliation Clinical Trials Research Centre, Department of Biostatistics, University of Liverpool, Liverpool, United Kingdom

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• B Hardwick,

  Roles Project administration, Writing – original draft, Writing – review & editing

  Affiliation Clinical Trials Research Centre, Department of Biostatistics, University of Liverpool, Liverpool, United Kingdom

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• H Hind,

  Roles Funding acquisition, Investigation, Methodology, Project administration

  Affiliation Clinical Trials Research Centre, Department of Biostatistics, University of Liverpool, Liverpool, United Kingdom

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• B Jacobs,

  Roles Data curation, Investigation, Writing – original draft, Writing – review & editing

  Affiliation Paediatrics, Royal National Orthopaedic Hospital, London, United Kingdom

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• D Vasileiou,

  Roles Formal analysis, Methodology, Software, Validation

  Affiliation Department of Mathematics and Statistics, Fylde College, Lancaster University, Lancaster, United Kingdom

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• I Wadsworth,

  Roles Formal analysis, Validation

  Affiliation Department of Mathematics and Statistics, Fylde College, Lancaster University, Lancaster, United Kingdom

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• N Ambrose,

  Roles Investigation, Writing – original draft, Writing – review & editing

  Affiliation Rheumatology, University College Hospital, London, United Kingdom

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• J Davidson,

  Roles Investigation, Writing – original draft, Writing – review & editing

  Affiliation Paediatric Rheumatology, Royal Hospital for Children, Glasgow, United Kingdom

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• P. J. Ferguson,

  Roles Investigation, Writing – original draft, Writing – review & editing

  Affiliation Stead Family Department of Pediatrics, University of Iowa Carver College of Medicine, Iowa City, IA, United States of America

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• T Herlin,

  Roles Investigation, Writing – original draft, Writing – review & editing

  Affiliation Department of Paediatrics, Aarhus University, Aarhus, Denmark

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• A Kavirayani,

  Roles Investigation, Writing – original draft, Writing – review & editing

  Affiliation Paediatric Rheumatology, Oxford University Hospitals NHS Foundation Trust, Oxford, United Kingdom

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• O. G. Killeen,

  Roles Investigation, Writing – original draft, Writing – review & editing

  Affiliation National Centre for Paediatric Rheumatology, Our Lady’s Children Hospital, Crumlin, Dublin, Ireland

  http://orcid.org/0000-0001-5780-6468

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• S Compeyrot-Lacassagne,

  Roles Conceptualization, Funding acquisition, Investigation, Writing – original draft, Writing – review & editing

  Affiliation Rheumatology, Great Ormond Street Hospital for Children NHS Foundation Trust, London, United Kingdom

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• R. M. Laxer,

  Roles Investigation, Writing – original draft, Writing – review & editing

  Affiliation Department of Paediatrics, University of Toronto, The Hospital for Sick Children, Toronto, Canada

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• M Roderick,

  Roles Investigation, Writing – original draft, Writing – review & editing

  Affiliation Paediatric Rheumatology, Bristol Royal Hospital for Children, Bristol and Bristol Medical School, University of Bristol, Bristol, United Kingdom

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• J. F. Swart,

  Roles Investigation, Writing – original draft, Writing – review & editing

  Affiliation Paediatric Rheumatology, University Medical Centre Utrecht, Utrecht, Netherlands

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• C. M. Hedrich,

  Roles Investigation, Writing – original draft, Writing – review & editing

  Affiliation Department of Women's & Children's Health, Institute of Translational Medicine, University of Liverpool, Liverpool, United Kingdom

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•  [ ... ],
• M. W. Beresford

  Roles Conceptualization, Data curation, Funding acquisition, Investigation, Methodology, Writing – original draft, Writing – review & editing

  Affiliations Department of Women's & Children's Health, Institute of Translational Medicine, University of Liverpool, Liverpool, United Kingdom, Department of Paediatric Rheumatology, Alder Hey Children’s NHS Foundation Trust, Liverpool, United Kingdom

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