Efficient design and analysis of randomized controlled trials in rare neurological diseases: An example in Guillain-Barré syndrome

• Nikki van Leeuwen ,

  Roles Formal analysis, Methodology, Writing – original draft

  * E-mail: n.vanleeuwen.1@erasmusmc.nl

  Affiliation Centre for Medical Decision Making, Department of Public Health, Erasmus University Medical Center, Rotterdam, The Netherlands

  http://orcid.org/0000-0002-3482-7335

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• Christa Walgaard,

  Roles Data curation, Writing – review & editing

  Affiliation Department of Neurology, Erasmus University Medical Center, Rotterdam, The Netherlands

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• Pieter A. van Doorn,

  Roles Data curation, Supervision, Writing – review & editing

  Affiliation Department of Neurology, Erasmus University Medical Center, Rotterdam, The Netherlands

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• Bart C. Jacobs,

  Roles Data curation, Supervision, Writing – review & editing

  Affiliations Department of Neurology, Erasmus University Medical Center, Rotterdam, The Netherlands, Department of Immunology, Erasmus University Medical Center, Rotterdam, The Netherlands

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• Ewout W. Steyerberg,

  Roles Methodology, Supervision, Writing – review & editing

  Affiliations Centre for Medical Decision Making, Department of Public Health, Erasmus University Medical Center, Rotterdam, The Netherlands, Department of Medical Statistics and Bioinformatics, Leiden University Medical Centre, Leiden, The Netherlands

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• Hester F. Lingsma

  Roles Methodology, Supervision, Writing – original draft

  Affiliation Centre for Medical Decision Making, Department of Public Health, Erasmus University Medical Center, Rotterdam, The Netherlands

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