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Open Access
Peer-reviewed
Research Article
The minor gentamicin complex component, X2, is a potent premature stop codon readthrough molecule with therapeutic potential
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Westley J. Friesen ,
Roles Conceptualization, Data curation, Formal analysis, Investigation, Methodology, Project administration, Supervision, Validation, Visualization, Writing – original draft, Writing – review & editing
* E-mail: wfriesen@ptcbio.com
Affiliation PTC Therapeutics, South Plainfield, NJ, United States of America
⨯ - Briana Johnson,
- Jairo Sierra,
- Jin Zhuo,
- Priya Vazirani,
- Xiaojiao Xue,
- Yuki Tomizawa,
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Ramil Baiazitov,
Roles Conceptualization, Investigation, Project administration, Supervision
Affiliation PTC Therapeutics, South Plainfield, NJ, United States of America
⨯ - Christie Morrill,
- Hongyu Ren,
- Suresh Babu,
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Young-Choon Moon,
Roles Conceptualization, Project administration, Supervision
Affiliation PTC Therapeutics, South Plainfield, NJ, United States of America
⨯ - Art Branstrom,
- Anna Mollin,
- Jean Hedrick,
- Josephine Sheedy,
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Gary Elfring,
Roles Formal analysis
Affiliation PTC Therapeutics, South Plainfield, NJ, United States of America
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Marla Weetall,
Roles Conceptualization, Project administration, Supervision
Affiliation PTC Therapeutics, South Plainfield, NJ, United States of America
⨯ - Joseph M. Colacino,
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Ellen M. Welch,
Roles Conceptualization, Project administration, Supervision
Affiliation PTC Therapeutics, South Plainfield, NJ, United States of America
⨯ - [ ... ],
- Stuart W. Peltz
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The minor gentamicin complex component, X2, is a potent premature stop codon readthrough molecule with therapeutic potential
- Westley J. Friesen,
- Briana Johnson,
- Jairo Sierra,
- Jin Zhuo,
- Priya Vazirani,
- Xiaojiao Xue,
- Yuki Tomizawa,
- Ramil Baiazitov,
- Christie Morrill,
- Hongyu Ren
- Published: October 25, 2018
- https://doi.org/10.1371/journal.pone.0206158