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Open Access
Peer-reviewed
Research Article
Impaired myogenic development, differentiation and function in hESC-derived SMA myoblasts and myotubes
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Nicole Hellbach,
Roles Conceptualization, Data curation, Formal analysis, Investigation, Methodology, Project administration, Supervision, Writing – original draft, Writing – review & editing
Affiliation Roche Innovation Center Basel, Roche pRED, Pharma Research & Early Development, Grenzacherstrasse, Basel, Switzerland
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Suzanne Peterson,
Roles Data curation, Formal analysis, Methodology
Affiliation Genea Biocells, North Torrey Pines Rd, San Diego, CA, United States of America
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Daniel Haehnke,
Roles Data curation, Formal analysis, Investigation, Methodology, Validation
Affiliation Roche Innovation Center Basel, Roche pRED, Pharma Research & Early Development, Grenzacherstrasse, Basel, Switzerland
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Aditi Shankar,
Roles Data curation, Formal analysis, Methodology
Affiliation Genea Biocells, North Torrey Pines Rd, San Diego, CA, United States of America
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Samuel LaBarge,
Roles Data curation, Formal analysis, Investigation, Methodology
Affiliation Genea Biocells, North Torrey Pines Rd, San Diego, CA, United States of America
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Cullen Pivaroff,
Roles Data curation, Formal analysis, Methodology
Affiliation Genea Biocells, North Torrey Pines Rd, San Diego, CA, United States of America
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Stefanie Saenger,
Roles Data curation, Formal analysis
Affiliation Roche Innovation Center Basel, Roche pRED, Pharma Research & Early Development, Grenzacherstrasse, Basel, Switzerland
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Carolin Thomas,
Roles Data curation, Formal analysis
Affiliation Roche Innovation Center Basel, Roche pRED, Pharma Research & Early Development, Grenzacherstrasse, Basel, Switzerland
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Kathleen McCarthy,
Roles Data curation, Investigation, Methodology, Supervision, Validation
Affiliation Roche Innovation Center Basel, Roche pRED, Pharma Research & Early Development, Grenzacherstrasse, Basel, Switzerland
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Martin Ebeling,
Roles Data curation, Investigation, Supervision, Validation
Affiliation Roche Innovation Center Basel, Roche pRED, Pharma Research & Early Development, Grenzacherstrasse, Basel, Switzerland
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Monica Hayhurst Bennett,
Roles Investigation, Writing – original draft, Writing – review & editing
Affiliation Genea Biocells, North Torrey Pines Rd, San Diego, CA, United States of America
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Uli Schmidt,
Roles Conceptualization, Investigation, Supervision, Validation, Writing – original draft, Writing – review & editing
Affiliation Genea Biocells, North Torrey Pines Rd, San Diego, CA, United States of America
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Friedrich Metzger
Roles Conceptualization, Data curation, Formal analysis, Funding acquisition, Resources, Supervision, Validation, Writing – original draft, Writing – review & editing
* E-mail: friedrich.metzger@versameb.com
Affiliation Roche Innovation Center Basel, Roche pRED, Pharma Research & Early Development, Grenzacherstrasse, Basel, Switzerland
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Impaired myogenic development, differentiation and function in hESC-derived SMA myoblasts and myotubes
- Nicole Hellbach,
- Suzanne Peterson,
- Daniel Haehnke,
- Aditi Shankar,
- Samuel LaBarge,
- Cullen Pivaroff,
- Stefanie Saenger,
- Carolin Thomas,
- Kathleen McCarthy,
- Martin Ebeling
- Published: October 10, 2018
- https://doi.org/10.1371/journal.pone.0205589