Antisense PMO cocktails effectively skip dystrophin exons 45-55 in myotubes transdifferentiated from DMD patient fibroblasts

• Joshua Lee,

  Roles Conceptualization, Formal analysis, Investigation, Writing – original draft, Writing – review & editing

  Affiliation Department of Medical Genetics, Faculty of Medicine and Dentistry, University of Alberta, Edmonton, AB, Canada

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• Yusuke Echigoya,

  Roles Formal analysis, Supervision, Writing – review & editing

  Affiliation Department of Veterinary Medicine, Nihon University, Fujisawa, Kanagawa, Japan

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• William Duddy,

  Roles Software

  Affiliation Northern Ireland Centre for Stratified Medicine, Altnagelvin Hospital Campus, Ulster University, Londonderry, United Kingdom

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• Takashi Saito,

  Roles Resources

  Affiliation Department of Molecular Therapy, National Institute of Neuroscience, National Center of Neurology and Psychiatry, Kodaira, Japan

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• Yoshitsugu Aoki,

  Roles Resources

  Affiliation Department of Molecular Therapy, National Institute of Neuroscience, National Center of Neurology and Psychiatry, Kodaira, Japan

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• Shin’ichi Takeda,

  Roles Resources

  Affiliation Department of Molecular Therapy, National Institute of Neuroscience, National Center of Neurology and Psychiatry, Kodaira, Japan

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• Toshifumi Yokota

  Roles Conceptualization, Formal analysis, Supervision, Writing – original draft, Writing – review & editing

  * E-mail: toshifum@ualberta.ca

  Affiliations Department of Medical Genetics, Faculty of Medicine and Dentistry, University of Alberta, Edmonton, AB, Canada, The Friends of Garrett Cumming Research & Muscular Dystrophy Canada HM Toupin Neurological Science Research Chair, Edmonton, AB, Canada

  http://orcid.org/0000-0001-7316-3546

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