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A dystrophic Duchenne mouse model for testing human antisense oligonucleotides
- Marcel Veltrop,
- Laura van Vliet,
- Margriet Hulsker,
- Jill Claassens,
- Conny Brouwers,
- Cor Breukel,
- Jos van der Kaa,
- Margot M. Linssen,
- Johan T. den Dunnen,
- Sjef Verbeek
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- Published: February 21, 2018
- https://doi.org/10.1371/journal.pone.0193289