Assessment of p.Phe508del-CFTR functional restoration in pediatric primary cystic fibrosis airway epithelial cells

• Erika N. Sutanto,

  Roles Data curation, Formal analysis, Investigation, Methodology, Writing – original draft

  Affiliations Telethon Kids Institute, the University of Western Australia, Nedlands, Western Australia, Australia, Department of Respiratory Medicine, Princess Margaret Hospital for Children, Perth, Western Australia, Australia

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• Amelia Scaffidi,

  Roles Data curation, Formal analysis, Methodology, Validation, Writing – review & editing

  Affiliation Office of Research Enterprise, The University of Western Australia, Nedlands, Western Australia, Australia

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• Luke W. Garratt,

  Roles Formal analysis, Investigation, Writing – review & editing

  Affiliation Telethon Kids Institute, the University of Western Australia, Nedlands, Western Australia, Australia

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• Kevin Looi,

  Roles Investigation, Writing – review & editing

  Affiliation Telethon Kids Institute, the University of Western Australia, Nedlands, Western Australia, Australia

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• Clara J. Foo,

  Roles Data curation, Investigation

  Affiliation School of Paediatrics and Child Health, The University of Western Australia, Nedlands, Western Australia, Australia

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• Michela A. Tessari,

  Roles Methodology, Resources, Writing – review & editing

  Affiliation Galapagos BV, 2300 AC, Leiden, the Netherlands

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• Richard A. Janssen,

  Roles Methodology, Resources, Writing – review & editing

  Affiliation Galapagos BV, 2300 AC, Leiden, the Netherlands

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• David F. Fischer,

  Roles Conceptualization, Methodology, Resources, Writing – review & editing

  Affiliation Charles River Laboratories, Leiden, the Netherlands

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• Stephen M. Stick ,

  Roles Conceptualization, Funding acquisition, Supervision, Writing – review & editing

  ¶‡ These authors are co senior authors on this work.

  Affiliations Telethon Kids Institute, the University of Western Australia, Nedlands, Western Australia, Australia, Department of Respiratory Medicine, Princess Margaret Hospital for Children, Perth, Western Australia, Australia, School of Paediatrics and Child Health, The University of Western Australia, Nedlands, Western Australia, Australia, Centre for Cell Therapy and Regenerative Medicine, School of Medicine and Pharmacology, The University of Western Australia, Nedlands, Western Australia, Australia

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• Anthony Kicic ,

  Roles Conceptualization, Data curation, Formal analysis, Supervision, Writing – review & editing

  * E-mail: Anthony.Kicic@telethonkids.org.au

  ¶‡ These authors are co senior authors on this work.

  Affiliations Telethon Kids Institute, the University of Western Australia, Nedlands, Western Australia, Australia, Department of Respiratory Medicine, Princess Margaret Hospital for Children, Perth, Western Australia, Australia, School of Paediatrics and Child Health, The University of Western Australia, Nedlands, Western Australia, Australia, Centre for Cell Therapy and Regenerative Medicine, School of Medicine and Pharmacology, The University of Western Australia, Nedlands, Western Australia, Australia

  http://orcid.org/0000-0002-0008-9733

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• on behalf of AREST CF

  ¶The full list of ARESTCF members is provided in the Acknowledgments.

  Affiliations Telethon Kids Institute, the University of Western Australia, Nedlands, Western Australia, Australia, Department of Respiratory Medicine, Princess Margaret Hospital for Children, Perth, Western Australia, Australia, Department of Respiratory Medicine, Royal Children’s Hospital, Melbourne, Australia, Murdoch Children’s Research Institute, Melbourne, Australia

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