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Long-term retinal cone rescue using a capsid mutant AAV8 vector in a mouse model of CNGA3-achromatopsia
- Xufeng Dai,
- Ying He,
- Hua Zhang,
- Yangyang Zhang,
- Yan Liu,
- Muran Wang,
- Hao Chen,
- Ji-jing Pang
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- Published: November 13, 2017
- https://doi.org/10.1371/journal.pone.0188032