Short (16-mer) locked nucleic acid splice-switching oligonucleotides restore dystrophin production in Duchenne Muscular Dystrophy myotubes

• Vanessa Borges Pires,

  Roles Formal analysis, Investigation, Methodology, Visualization, Writing – original draft

  Affiliation Instituto de Medicina Molecular, Faculdade de Medicina, Universidade de Lisboa, Lisboa, Portugal

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• Ricardo Simões,

  Roles Conceptualization, Investigation, Methodology

  Affiliation Instituto de Medicina Molecular, Faculdade de Medicina, Universidade de Lisboa, Lisboa, Portugal

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• Kamel Mamchaoui,

  Roles Methodology, Resources

  Affiliation Center for Research in Myology, INSERM UMRS974, CNRS FRE3617, Sorbonne Universités, UPMC Univ Paris 06, Paris, France

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• Célia Carvalho ,

  Contributed equally to this work with: Célia Carvalho, Maria Carmo-Fonseca

  Roles Conceptualization, Investigation, Methodology, Supervision, Validation, Writing – original draft, Writing – review & editing

  * E-mail: carmo.fonseca@medicina.ulisboa.pt (MCF); hcelia@medicina.ulisboa.pt (CC)

  Affiliation Instituto de Medicina Molecular, Faculdade de Medicina, Universidade de Lisboa, Lisboa, Portugal

  http://orcid.org/0000-0002-5980-595X

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• Maria Carmo-Fonseca

  Contributed equally to this work with: Célia Carvalho, Maria Carmo-Fonseca

  Roles Conceptualization, Funding acquisition, Project administration, Supervision, Validation, Writing – original draft, Writing – review & editing

  * E-mail: carmo.fonseca@medicina.ulisboa.pt (MCF); hcelia@medicina.ulisboa.pt (CC)

  Affiliation Instituto de Medicina Molecular, Faculdade de Medicina, Universidade de Lisboa, Lisboa, Portugal

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