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Histopathological Defects in Intestine in Severe Spinal Muscular Atrophy Mice Are Improved by Systemic Antisense Oligonucleotide Treatment
- Palittiya Sintusek,
- Francesco Catapano,
- Napat Angkathunkayul,
- Elena Marrosu,
- Simon H. Parson,
- Jennifer E. Morgan,
- Francesco Muntoni,
- Haiyan Zhou
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- Published: May 10, 2016
- https://doi.org/10.1371/journal.pone.0155032