Oral Migalastat HCl Leads to Greater Systemic Exposure and Tissue Levels of Active α-Galactosidase A in Fabry Patients when Co-Administered with Infused Agalsidase

• David G. Warnock,

  Affiliation University of Alabama at Birmingham School of Medicine Department of Medicine, Division of Nephrology, Birmingham, Alabama, United States of America

  ⨯
• Daniel G. Bichet,

  Affiliation University of Montreal, Quebec, Canada

  ⨯
• Myrl Holida,

  Affiliation University of Iowa Children’s Hospital, Iowa City, Iowa, United States of America

  ⨯
• Ozlem Goker-Alpan,

  Affiliation LSD Research and Treatment Unit, O&O Alpan LLC, Fairfax, Virginia, United States of America

  ⨯
• Kathy Nicholls,

  Affiliation Department of Nephrology, Royal Melbourne Hospital, and University of Melbourne, Parkville, Victoria, Australia

  ⨯
• Mark Thomas,

  Affiliation Linear Clinical Research Ltd, Queen Elizabeth II Medical Centre, and University of Western Australia, Nedlands, Western Australia

  ⨯
• Francois Eyskens,

  Affiliation Universitair Ziekenhuis Antwerpen, Antwerpen, Belgium

  ⨯
• Suma Shankar,

  Affiliation Emory University School of Medicine, Emory Genetics Clinic, Athens, Georgia, United States of America

  ⨯
• Mathews Adera,

  Affiliation Amicus Therapeutics, Cranbury, New Jersey, United States of America

  ⨯
• Sheela Sitaraman,

  Affiliation Amicus Therapeutics, Cranbury, New Jersey, United States of America

  ⨯
• Richie Khanna,

  Affiliation Amicus Therapeutics, Cranbury, New Jersey, United States of America

  ⨯
• John J. Flanagan,

  Affiliation Arvinas Inc, New Haven, Connecticut, United States of America

  ⨯
• Brandon A. Wustman,

  Affiliation Institute and Clinical Center, Sunnyvale, California, United States of America

  ⨯
• Jay Barth,

  Affiliation Amicus Therapeutics, Cranbury, New Jersey, United States of America

  ⨯
• Carrolee Barlow,

  Affiliation Amicus Therapeutics, Cranbury, New Jersey, United States of America

  ⨯
• Kenneth J. Valenzano,

  Affiliation Amicus Therapeutics, Cranbury, New Jersey, United States of America

  ⨯
• David J. Lockhart,

  Affiliation Institute and Clinical Center, Sunnyvale, California, United States of America

  ⨯
• Pol Boudes,

  Affiliation Cymabay Therapeutics, Newark, California, United States of America

  ⨯
•  [ ... ],
• Franklin K. Johnson

  * E-mail: fjohnson@amicusrx.com

  Affiliation Amicus Therapeutics, Cranbury, New Jersey, United States of America

  ⨯
• [ view all ]
• [ view less ]