Characterization of Early Disease Status in Treatment-Naive Male Paediatric Patients with Fabry Disease Enrolled in a Randomized Clinical Trial

• Frits A. Wijburg,

  Affiliation Academic Medical Center, University Hospital of Amsterdam, Amsterdam, The Netherlands

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• Bernard Bénichou,

  Affiliation Genzyme Europe, Saint-Germain-en-Laye, France

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• Daniel G. Bichet,

  Affiliation Hôpital du Sacré-Cœur de Montréal and University of Montreal, Montreal, QC, Canada

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• Lorne A. Clarke,

  Affiliation University of British Columbia, Child and Family Research Institute, Vancouver, BC, Canada

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• Gabriela Dostalova,

  Affiliation Charles University Prague, General University Hospital Prague, Prague, Czech Republic

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• Alejandro Fainboim,

  Affiliation Hospital de Niños Ricardo Gutierrez, Hospital de Día Polivalente, Ciudad Autónoma de Buenos Aires, Argentina

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• Andreas Fellgiebel,

  Affiliation University Medical Center Mainz, Mainz, Germany

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• Cassiano Forcelini,

  Affiliation Hospital São Vicente de Paulo, Passo Fundo, RS, Brazil

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• Kristina An Haack,

  Affiliation Sanofi, Chilly-Mazarin, France

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• Robert J. Hopkin,

  Affiliation Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, United States of America

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• Michael Mauer,

  Affiliation Departments of Pediatrics and Medicine, University of Minnesota, Minneapolis, Minnesota, United States of America

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• Behzad Najafian,

  Affiliation Department of Pathology, University of Washington, Seattle, Washington, United States of America

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• C. Ronald Scott,

  Affiliation University of Washington School of Medicine, Seattle, Washington, United States of America

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• Suma P. Shankar,

  Affiliation Emory University School of Medicine, Decatur, Georgia, United States of America

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• Beth L. Thurberg,

  Affiliation Department of Pathology, Genzyme, Framingham, Massachusetts, United States of America

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• Camilla Tøndel,

  Affiliation Department of Pediatrics, Haukeland University Hospital, Bergen, Norway

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• Anna Tylki-Szymańska,

  Affiliation Klinika Pediatrii, Żywienia i Chorób Metabolicznych Instytut “Pomnik – Centrum Zdrowia Dziecka”, Warsaw, Poland

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•  [ ... ],
• Uma Ramaswami

  * E-mail: uma.ramaswami@nhs.net

  Affiliation Royal Free Hospital, London, United Kingdom

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