Rapamycin and Chloroquine: The In Vitro and In Vivo Effects of Autophagy-Modifying Drugs Show Promising Results in Valosin Containing Protein Multisystem Proteinopathy

• Angèle Nalbandian ,

  * E-mail: a.nalbandian@uci.edu (AN); vkimonis@uci.edu (VEK)

  Affiliations Department of Pediatrics, Division of Genetics and Metabolism, University of California, Irvine, California, United States of America, Sue and Bill Gross Stem Cell Center, University of California, Irvine, California, United States of America

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• Katrina J. Llewellyn,

  Affiliations Department of Pediatrics, Division of Genetics and Metabolism, University of California, Irvine, California, United States of America, Sue and Bill Gross Stem Cell Center, University of California, Irvine, California, United States of America

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• Christopher Nguyen,

  Affiliation Department of Pediatrics, Division of Genetics and Metabolism, University of California, Irvine, California, United States of America

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• Puya G. Yazdi,

  Affiliations Sue and Bill Gross Stem Cell Center, University of California, Irvine, California, United States of America, Systomic Health LLC, Los Angeles, California, United States of America

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• Virginia E. Kimonis

  * E-mail: a.nalbandian@uci.edu (AN); vkimonis@uci.edu (VEK)

  Affiliations Department of Pediatrics, Division of Genetics and Metabolism, University of California, Irvine, California, United States of America, Sue and Bill Gross Stem Cell Center, University of California, Irvine, California, United States of America

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