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Delivery of Full-Length Factor VIII Using a piggyBac Transposon Vector to Correct a Mouse Model of Hemophilia A
- Hideto Matsui,
- Naoko Fujimoto,
- Noriko Sasakawa,
- Yasuhide Ohinata,
- Midori Shima,
- Shinya Yamanaka,
- Mitsuhiko Sugimoto,
- Akitsu Hotta
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- Published: August 15, 2014
- https://doi.org/10.1371/journal.pone.0104957