Dose Responsive Effects of Subcutaneous Pentosan Polysulfate Injection in Mucopolysaccharidosis Type VI Rats and Comparison to Oral Treatment

• Michael Frohbergh,

  Affiliation Genetics and Genomic Sciences, Icahn School of Medicine at Mount Sinai, New York, New York, United States of America

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• Yi Ge,

  Affiliation Genetics and Genomic Sciences, Icahn School of Medicine at Mount Sinai, New York, New York, United States of America

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• Fanli Meng,

  Affiliation Genetics and Genomic Sciences, Icahn School of Medicine at Mount Sinai, New York, New York, United States of America

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• Nesrin Karabul,

  Affiliation Department of Pediatrics, University of Mainz, Mainz, Germany

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• Alexander Solyom,

  Affiliations Department of Pediatrics, University of Mainz, Mainz, Germany, Department of Pediatrics, University of Pécs, Pécs, Hungary

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• Alon Lai,

  Affiliation Orthopedics, Icahn School of Medicine at Mount Sinai, New York, New York, United States of America

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• James Iatridis,

  Affiliation Orthopedics, Icahn School of Medicine at Mount Sinai, New York, New York, United States of America

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• Edward H. Schuchman,

  Affiliation Genetics and Genomic Sciences, Icahn School of Medicine at Mount Sinai, New York, New York, United States of America

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• Calogera M. Simonaro

  * E-mail: calogera.simonaro@mssm.edu

  Affiliation Genetics and Genomic Sciences, Icahn School of Medicine at Mount Sinai, New York, New York, United States of America

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