Rescue of the Friedreich Ataxia Knockout Mutation in Transgenic Mice Containing an FXN-EGFP Genomic Reporter

• Joseph P. Sarsero ,

  * E-mail: joe@sarsero.com

  Affiliations Cell and Gene Therapy, Murdoch Childrens Research Institute, Royal Children’s Hospital, Parkville, Victoria, Australia, Department of Paediatrics, The University of Melbourne, Royal Children’s Hospital, Parkville, Victoria, Australia

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• Timothy P. Holloway,

  Affiliation Cell and Gene Therapy, Murdoch Childrens Research Institute, Royal Children’s Hospital, Parkville, Victoria, Australia

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• Lingli Li,

  Affiliation Cell and Gene Therapy, Murdoch Childrens Research Institute, Royal Children’s Hospital, Parkville, Victoria, Australia

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• David I. Finkelstein,

  Affiliation Florey Institute of Neuroscience and Mental Health, The University of Melbourne, Victoria, Australia

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• Panos A. Ioannou †

  † Deceased.

  Affiliations Cell and Gene Therapy, Murdoch Childrens Research Institute, Royal Children’s Hospital, Parkville, Victoria, Australia, Department of Paediatrics, The University of Melbourne, Royal Children’s Hospital, Parkville, Victoria, Australia

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