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Effective Exon Skipping and Dystrophin Restoration by 2′-O-Methoxyethyl Antisense Oligonucleotide in Dystrophin-Deficient Mice
- Lu Yang,
- Hongjing Niu,
- Xianjun Gao,
- Qingsong Wang,
- Gang Han,
- Limin Cao,
- Chunquan Cai,
- Jan Weiler,
- Haifang Yin
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- Published: April 26, 2013
- https://doi.org/10.1371/journal.pone.0061584