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Impact of Age at Administration, Lysosomal Storage, and Transgene Regulatory Elements on AAV2/8-Mediated Rat Liver Transduction
- Gabriella Cotugno,
- Patrizia Annunziata,
- Maria Vittoria Barone,
- Marianthi Karali,
- Sandro Banfi,
- Alberto Auricchio
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- Published: March 13, 2012
- https://doi.org/10.1371/journal.pone.0033286