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Protein Replacement Therapy Partially Corrects the Cholesterol-Storage Phenotype in a Mouse Model of Niemann-Pick Type C2 Disease
- Gitte Krogh Nielsen,
- Frederik Dagnaes-Hansen,
- Ida Elisabeth Holm,
- Steve Meaney,
- Derek Symula,
- Niels Trolle Andersen,
- Christian Würtz Heegaard
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- Published: November 3, 2011
- https://doi.org/10.1371/journal.pone.0027287