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Targeting Several CAG Expansion Diseases by a Single Antisense Oligonucleotide
- Melvin M. Evers,
- Barry A. Pepers,
- Judith C. T. van Deutekom,
- Susan A. M. Mulders,
- Johan T. den Dunnen,
- Annemieke Aartsma-Rus,
- Gert-Jan B. van Ommen,
- Willeke M. C. van Roon-Mom
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- Published: September 1, 2011
- https://doi.org/10.1371/journal.pone.0024308