Characterization of Dysferlin Deficient SJL/J Mice to Assess Preclinical Drug Efficacy: Fasudil Exacerbates Muscle Disease Phenotype

• Sree Rayavarapu,

  Affiliations Center for Genetic Medicine Research, Children's National Medical Center, Washington, D.C., United States of America, Institute of Biomedical Sciences, The George Washington University, Washington, D.C., United States of America

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• Jack H. Van der meulen,

  Affiliation Center for Genetic Medicine Research, Children's National Medical Center, Washington, D.C., United States of America

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• Heather Gordish-Dressman,

  Affiliation Center for Genetic Medicine Research, Children's National Medical Center, Washington, D.C., United States of America

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• Eric P. Hoffman,

  Affiliations Center for Genetic Medicine Research, Children's National Medical Center, Washington, D.C., United States of America, Department of Integrative Systems Biology, School of Medicine and Health Sciences, The George Washington University, Washington, D.C., United States of America

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• Kanneboyina Nagaraju ,

  * E-mail: KNagaraju@cnmcresearch.org (KN); sknoblach@cnmcresearch.org (SMK)

  Affiliations Center for Genetic Medicine Research, Children's National Medical Center, Washington, D.C., United States of America, Department of Integrative Systems Biology, School of Medicine and Health Sciences, The George Washington University, Washington, D.C., United States of America

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• Susan M. Knoblach

  * E-mail: KNagaraju@cnmcresearch.org (KN); sknoblach@cnmcresearch.org (SMK)

  Affiliations Center for Genetic Medicine Research, Children's National Medical Center, Washington, D.C., United States of America, Department of Integrative Systems Biology, School of Medicine and Health Sciences, The George Washington University, Washington, D.C., United States of America

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