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AAV delivery of GBA1 suppresses α-synuclein accumulation in Parkinson’s disease models and restores functions in Gaucher’s disease models
Okai T,
Sato S,
Deshpande M,
Matsumoto Si,
Nakayama M,
et al.
(2025)
AAV delivery of GBA1 suppresses α-synuclein accumulation in Parkinson’s disease models and restores functions in Gaucher’s disease models.
PLOS ONE 20(5): e0321145.
https://doi.org/10.1371/journal.pone.0321145