About the Authors

Kate Maresh

Roles Conceptualization, Data curation, Formal analysis, Funding acquisition, Investigation, Methodology, Project administration, Resources, Writing – original draft, Writing – review & editing

Affiliations Dubowitz Neuromuscular Centre, UCL Great Ormond Street Institute of Child Health, London, United Kingdom, MRC Centre for Neuromuscular Diseases, UCL, London, United Kingdom

Andriani Papageorgiou

Roles Data curation, Formal analysis, Investigation, Methodology, Writing – original draft, Writing – review & editing

Affiliation Dubowitz Neuromuscular Centre, UCL Great Ormond Street Institute of Child Health, London, United Kingdom

Deborah Ridout

Roles Formal analysis, Methodology, Supervision, Writing – review & editing

Affiliations Department of Population, Policy & Practice, UCL Great Ormond Street Institute of Child Health, London, United Kingdom, NIHR Great Ormond Street Hospital Biomedical Research Centre, Great Ormond Street Institute of Child Health, University College London, & Great Ormond Street Hospital Trust, London, United Kingdom

Neil Harrison

Roles Conceptualization, Methodology, Writing – review & editing

Affiliation Division of Psychological Medicine and Clinical Neurosciences, Cardiff University, Cardiff, United Kingdom

William Mandy

Roles Conceptualization, Methodology, Supervision, Writing – review & editing

Affiliation Department of Clinical, Educational and Health Psychology, UCL, London, United Kingdom

David Skuse

Roles Conceptualization, Methodology, Supervision, Writing – review & editing

Affiliation Department of Behavioural and Brain Sciences, UCL Great Ormond Street Institute of Child Health, London, United Kingdom

Francesco Muntoni

Roles Conceptualization, Funding acquisition, Methodology, Resources, Supervision, Writing – review & editing

f.muntoni@ucl.ac.uk

Affiliations Dubowitz Neuromuscular Centre, UCL Great Ormond Street Institute of Child Health, London, United Kingdom, MRC Centre for Neuromuscular Diseases, UCL, London, United Kingdom, NIHR Great Ormond Street Hospital Biomedical Research Centre, Great Ormond Street Institute of Child Health, University College London, & Great Ormond Street Hospital Trust, London, United Kingdom

Competing Interests

I have read the journal’s policy and the authors of this manuscript have the following competing interests: FM has received grants, speaker and consultancy honoraria from Sarepta Therapeutics, Avexis, PTC Therapeutics, Roche, Biogen, Dyne Therapeutics, Novartis and Pfizer; DS has current grant funding from the Medical Research Council (UK), Sarepta Therapeutics, the European Research Council, and the Patrick Paul Foundation; WM is supported by the National Institute of Health Research, Autistica, the Dunhill Medical Trust, the Medical Research Council and the European Research Council; NH has received consulting fees from Janssen and GSK. The remaining authors have declared no competing interests.