About the Authors

Paul T. Martin

Roles Conceptualization, Formal analysis, Funding acquisition, Investigation, Methodology, Supervision, Writing – original draft, Writing – review & editing

Paul.Martin@nationwidechildrens.org

Affiliations Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children’s Hospital, Columbus, Ohio, United States of America, Department of Pediatrics, The Ohio State University College of Medicine, Columbus, Ohio, United States of America

Deborah A. Zygmunt

Roles Formal analysis, Investigation, Methodology, Writing – original draft, Writing – review & editing

Affiliation Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children’s Hospital, Columbus, Ohio, United States of America

Anna Ashbrook

Roles Investigation, Writing – review & editing

Affiliation Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children’s Hospital, Columbus, Ohio, United States of America

Sonia Hamilton

Roles Investigation, Writing – review & editing

Affiliation Neuroscience Undergraduate Program, The Ohio State University, Columbus, Ohio, United States of America

Davin Packer

Roles Investigation, Writing – review & editing

Affiliation Neuroscience Graduate Program, The Ohio State University, Columbus, Ohio, United States of America

Sharla M. Birch

Roles Investigation, Resources, Writing – review & editing

Affiliation Department of Veterinary Integrative Biosciences, College of Veterinary Medicine and Biomedical Sciences, Texas A&M University, College Station, TX, United States of America

Amanda K. Bettis

Roles Investigation, Writing – review & editing

Affiliation Department of Veterinary Integrative Biosciences, College of Veterinary Medicine and Biomedical Sciences, Texas A&M University, College Station, TX, United States of America

Cynthia J. Balog-Alvarez

Roles Investigation, Writing – review & editing

Affiliation Department of Veterinary Integrative Biosciences, College of Veterinary Medicine and Biomedical Sciences, Texas A&M University, College Station, TX, United States of America

Lee-Jae Guo

Roles Formal analysis, Investigation, Writing – original draft, Writing – review & editing

Affiliation Department of Veterinary Integrative Biosciences, College of Veterinary Medicine and Biomedical Sciences, Texas A&M University, College Station, TX, United States of America

Peter P. Nghiem

Roles Investigation, Writing – original draft, Writing – review & editing

Affiliation Department of Veterinary Integrative Biosciences, College of Veterinary Medicine and Biomedical Sciences, Texas A&M University, College Station, TX, United States of America

Joe N. Kornegay

Roles Conceptualization, Formal analysis, Investigation, Methodology, Project administration, Resources, Supervision, Writing – original draft, Writing – review & editing

Affiliation Department of Veterinary Integrative Biosciences, College of Veterinary Medicine and Biomedical Sciences, Texas A&M University, College Station, TX, United States of America

Competing Interests

PTM has a financial conflict of interest with regard to the publication of this work, as he receives licensing fees from Sarepta Therapeutics for rAAVrh74.MCK.GALGT2. PTM is also President and CSO of Genosera, Inc. JNK is a paid consultant for Solid Biosciences. PPN is a paid consultant for AGADA Biosciences. None of the other authors have any conflict to report. This does not alter our adherence to PLOS ONE policies on sharing data and materials.