About the Authors
- Paul T. Martin
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Roles Conceptualization, Formal analysis, Funding acquisition, Investigation, Methodology, Supervision, Writing – original draft, Writing – review & editing
* E-mail: Paul.Martin@nationwidechildrens.org
Affiliations Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children’s Hospital, Columbus, Ohio, United States of America, Department of Pediatrics, The Ohio State University College of Medicine, Columbus, Ohio, United States of America
- Deborah A. Zygmunt
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Roles Formal analysis, Investigation, Methodology, Writing – original draft, Writing – review & editing
Affiliation Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children’s Hospital, Columbus, Ohio, United States of America
- Anna Ashbrook
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Roles Investigation, Writing – review & editing
Affiliation Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children’s Hospital, Columbus, Ohio, United States of America
- Sonia Hamilton
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Roles Investigation, Writing – review & editing
Affiliation Neuroscience Undergraduate Program, The Ohio State University, Columbus, Ohio, United States of America
- Davin Packer
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Roles Investigation, Writing – review & editing
Affiliation Neuroscience Graduate Program, The Ohio State University, Columbus, Ohio, United States of America
- Sharla M. Birch
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Roles Investigation, Resources, Writing – review & editing
Affiliation Department of Veterinary Integrative Biosciences, College of Veterinary Medicine and Biomedical Sciences, Texas A&M University, College Station, TX, United States of America
- Amanda K. Bettis
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Roles Investigation, Writing – review & editing
Affiliation Department of Veterinary Integrative Biosciences, College of Veterinary Medicine and Biomedical Sciences, Texas A&M University, College Station, TX, United States of America
- Cynthia J. Balog-Alvarez
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Roles Investigation, Writing – review & editing
Affiliation Department of Veterinary Integrative Biosciences, College of Veterinary Medicine and Biomedical Sciences, Texas A&M University, College Station, TX, United States of America
- Lee-Jae Guo
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Roles Formal analysis, Investigation, Writing – original draft, Writing – review & editing
Affiliation Department of Veterinary Integrative Biosciences, College of Veterinary Medicine and Biomedical Sciences, Texas A&M University, College Station, TX, United States of America
- Peter P. Nghiem
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Roles Investigation, Writing – original draft, Writing – review & editing
Affiliation Department of Veterinary Integrative Biosciences, College of Veterinary Medicine and Biomedical Sciences, Texas A&M University, College Station, TX, United States of America
- Joe N. Kornegay
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Roles Conceptualization, Formal analysis, Investigation, Methodology, Project administration, Resources, Supervision, Writing – original draft, Writing – review & editing
Affiliation Department of Veterinary Integrative Biosciences, College of Veterinary Medicine and Biomedical Sciences, Texas A&M University, College Station, TX, United States of America
Competing Interests
PTM has a financial conflict of interest with regard to the publication of this work, as he receives licensing fees from Sarepta Therapeutics for rAAVrh74.MCK.GALGT2. PTM is also President and CSO of Genosera, Inc. JNK is a paid consultant for Solid Biosciences. PPN is a paid consultant for AGADA Biosciences. None of the other authors have any conflict to report. This does not alter our adherence to PLOS ONE policies on sharing data and materials.