About the Authors

Catlyn Cavender

Roles Formal analysis, Investigation, Writing – original draft

Affiliation Research, BioMarin Pharmaceutical Inc., Novato, CA, United States of America

Linley Mangini

Roles Methodology, Writing – original draft

Affiliation Research, BioMarin Pharmaceutical Inc., Novato, CA, United States of America

Jeremy L. Van Vleet

Roles Methodology, Writing – original draft

Affiliation Research, BioMarin Pharmaceutical Inc., Novato, CA, United States of America

Carley Corado

Roles Conceptualization, Resources

Affiliation Research, BioMarin Pharmaceutical Inc., Novato, CA, United States of America

Emma McCullagh

Roles Conceptualization, Resources

Affiliation Research, BioMarin Pharmaceutical Inc., Novato, CA, United States of America

Heather L. Gray-Edwards

Roles Conceptualization, Resources

Affiliation University of Massachusetts Medical School, Worcester, MA, United States of America

Douglas R. Martin

Roles Conceptualization, Resources, Writing – review & editing

Affiliation Scott-Ritchey Research Center and Department of Anatomy, Physiology, and Pharmacology, Auburn University College of Veterinary Medicine, Auburn, AL, United States of America

Brett E. Crawford

Roles Resources, Supervision, Writing – review & editing

Affiliation Research, BioMarin Pharmaceutical Inc., Novato, CA, United States of America

Roger Lawrence

Roles Data curation, Formal analysis, Project administration, Supervision, Writing – review & editing

rlawrence@bmrn.com

Affiliation Research, BioMarin Pharmaceutical Inc., Novato, CA, United States of America

Competing Interests

CC was a consultant of BioMarin Pharmaceutical Inc. LM, JVV, CC, EM, BEC, and RL are employees of and have interest in BioMarin Pharmaceutical Inc. HLG and DRM have collaborated with BioMarin Pharmaceutical Inc. during and outside of the conduct of this study. This does not alter our adherence to PLOS ONE policies on sharing data and materials.