About the Authors

Mangala M. Soundarapandian

Roles Conceptualization, Data curation, Formal analysis, Investigation, Methodology, Writing – review & editing

msoundar@alnylam.com (MMS); deleon@email.chop.edu (DDDL)

Affiliation Alnylam Pharmaceuticals, Cambridge, Massachusetts, United States of America

Christine A. Juliana

Roles Data curation, Formal analysis, Writing – original draft

Affiliation Division of Endocrinology and Diabetes, The Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States of America

Jinghua Chai

Roles Investigation

Affiliation Division of Endocrinology and Diabetes, The Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States of America

Patrick A. Haslett

Roles Conceptualization, Writing – review & editing

Affiliation Alnylam Pharmaceuticals, Cambridge, Massachusetts, United States of America

Kevin Fitzgerald

Roles Conceptualization, Writing – review & editing

Affiliation Alnylam Pharmaceuticals, Cambridge, Massachusetts, United States of America

Diva D. De León

Roles Conceptualization, Methodology, Project administration, Supervision, Writing – review & editing

msoundar@alnylam.com (MMS); deleon@email.chop.edu (DDDL)

Affiliations Division of Endocrinology and Diabetes, The Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States of America, Department of Pediatrics, Perelman School of Medicine at the University of Pennsylvania, Philadelphia, Pennsylvania, United States of America

Competing Interests

MMS, PAH and KF work for Alnylam Pharamaceuticals; MMS, PAH and KF hold shares in Alnylam Pharmaceuticals stock; DDDL received funding from Alnylam Pharmaceuticals to conduct this study. We confirm that this does not alter our adherence to the PLOS ONE policies on sharing data and materials and have updated our Competing Interests statement.