About the Authors

Jacqueline Montes

Roles Conceptualization, Data curation, Investigation, Methodology, Project administration, Writing – original draft, Writing – review & editing

jm598@columbia.edu

Affiliations Departments of Neurology, Columbia University Medical Center, New York, NY, United States of America, Rehabilitation and Regenerative Medicine, Columbia University Medical Center, New York, NY, United States of America

Michael P. McDermott

Roles Conceptualization, Data curation, Formal analysis, Funding acquisition, Methodology, Writing – original draft, Writing – review & editing

Affiliations Department of Neurology, University of Rochester, Rochester, NY, United States of America, Department of Biostatistics and Computational Biology, University of Rochester, Rochester, NY, United States of America

Elizabeth Mirek

Roles Data curation, Investigation, Writing – review & editing

Affiliations Department of Neurology, Boston Children’s Hospital, Harvard Medical School, Boston, MA, United States of America, Department of Physical Therapy and Occupational Therapy Services, Boston Children’s Hospital, Boston, MA, United States of America

Elena S. Mazzone

Roles Conceptualization, Data curation, Investigation, Methodology, Writing – review & editing

Affiliation Department of Paediatric Neurology and Nemo Clinical Centre, Catholic University, Rome, Italy

Marion Main

Roles Conceptualization, Data curation, Investigation, Project administration, Writing – review & editing

Affiliation Dubowitz Neuromuscular Centre, UCL Great Ormond Street Institute of Child Health, London, United Kingdom

Allan M. Glanzman

Roles Conceptualization, Data curation, Investigation, Methodology, Writing – review & editing

Affiliation Department of Physical Therapy, The Children’s Hospital of Philadelphia, Philadelphia, PA, United States of America

Tina Duong

Roles Conceptualization, Data curation, Investigation, Writing – review & editing

Affiliation Departments of Neurology and Pediatrics, Stanford University School of Medicine, Stanford, CA, United States of America

Sally Dunaway Young

Roles Conceptualization, Data curation, Investigation, Methodology, Writing – review & editing

Affiliations Departments of Neurology, Columbia University Medical Center, New York, NY, United States of America, Rehabilitation and Regenerative Medicine, Columbia University Medical Center, New York, NY, United States of America

Rachel Salazar

Roles Conceptualization, Data curation, Investigation, Writing – review & editing

Affiliation Departments of Neurology, Columbia University Medical Center, New York, NY, United States of America

Amy Pasternak

Roles Conceptualization, Data curation, Investigation, Methodology, Writing – review & editing

Affiliations Department of Neurology, Boston Children’s Hospital, Harvard Medical School, Boston, MA, United States of America, Department of Physical Therapy and Occupational Therapy Services, Boston Children’s Hospital, Boston, MA, United States of America

Richard Gee

Roles Conceptualization, Data curation, Methodology, Writing – review & editing

Affiliation Departments of Neurology and Pediatrics, Stanford University School of Medicine, Stanford, CA, United States of America

Roberto De Sanctis

Roles Conceptualization, Data curation, Investigation, Writing – review & editing

Affiliation Department of Paediatric Neurology and Nemo Clinical Centre, Catholic University, Rome, Italy

Giorgia Coratti

Roles Conceptualization, Data curation, Investigation, Methodology, Writing – review & editing

Affiliation Department of Paediatric Neurology and Nemo Clinical Centre, Catholic University, Rome, Italy

Nicola Forcina

Roles Conceptualization, Data curation, Investigation, Writing – review & editing

Affiliation Department of Paediatric Neurology and Nemo Clinical Centre, Catholic University, Rome, Italy

Lavinia Fanelli

Roles Conceptualization, Data curation, Investigation, Writing – review & editing

Affiliation Department of Paediatric Neurology and Nemo Clinical Centre, Catholic University, Rome, Italy

Danielle Ramsey

Roles Conceptualization, Data curation, Investigation, Writing – review & editing

Affiliation Dubowitz Neuromuscular Centre, UCL Great Ormond Street Institute of Child Health, London, United Kingdom

Evelin Milev

Roles Conceptualization, Data curation, Investigation, Writing – review & editing

Affiliation Dubowitz Neuromuscular Centre, UCL Great Ormond Street Institute of Child Health, London, United Kingdom

Matthew Civitello

Roles Conceptualization, Data curation, Methodology, Writing – review & editing

Affiliation Nemours Children’s Hospital, Orlando, FL, United States of America

Marika Pane

Roles Conceptualization, Data curation, Investigation, Methodology, Writing – review & editing

Affiliation Department of Paediatric Neurology and Nemo Clinical Centre, Catholic University, Rome, Italy

Maria Carmela Pera

Roles Conceptualization, Data curation, Investigation, Methodology, Writing – review & editing

Affiliation Department of Paediatric Neurology and Nemo Clinical Centre, Catholic University, Rome, Italy

Mariacristina Scoto

Roles Conceptualization, Data curation, Investigation, Methodology, Writing – review & editing

Affiliation Dubowitz Neuromuscular Centre, UCL Great Ormond Street Institute of Child Health, London, United Kingdom

John W. Day

Roles Conceptualization, Data curation, Funding acquisition, Investigation, Methodology, Writing – review & editing

Affiliation Departments of Neurology and Pediatrics, Stanford University School of Medicine, Stanford, CA, United States of America

Gihan Tennekoon

Roles Conceptualization, Data curation, Funding acquisition, Investigation, Methodology, Writing – review & editing

Affiliation Departments of Neurology, Pediatrics, The Children’s Hospital of Philadelphia, University of Pennsylvania, Philadelphia, PA, United States of America

Richard S. Finkel

Roles Conceptualization, Data curation, Funding acquisition, Investigation, Methodology, Writing – review & editing

Affiliation Nemours Children’s Hospital, Orlando, FL, United States of America

Basil T. Darras

Roles Conceptualization, Data curation, Funding acquisition, Investigation, Methodology, Writing – review & editing

Affiliation Department of Neurology, Boston Children’s Hospital, Harvard Medical School, Boston, MA, United States of America

Francesco Muntoni

Roles Conceptualization, Data curation, Funding acquisition, Methodology, Writing – review & editing

Affiliation Dubowitz Neuromuscular Centre, UCL Great Ormond Street Institute of Child Health, London, United Kingdom

Darryl C. De Vivo

Roles Conceptualization, Data curation, Funding acquisition, Methodology, Writing – review & editing

Affiliation Departments of Neurology, Columbia University Medical Center, New York, NY, United States of America

Eugenio Mercuri

Roles Conceptualization, Data curation, Funding acquisition, Methodology, Writing – original draft, Writing – review & editing

Affiliation Department of Paediatric Neurology and Nemo Clinical Centre, Catholic University, Rome, Italy

Competing Interests

The authors have declared that no competing interests exist.